Design Therapeutics

Design Therapeutics(DSGN)

CARLSBAD, CA
Biotechnology

Focus: Drugs targeting disorders caused by nucleotide-repeat expansions

Design Therapeutics is a life sciences company focused on Drugs targeting disorders caused by nucleotide-repeat expansions.

OncologyNeurologyInfectious DiseasesCardiovascularRespiratory
Funding Stage
PUBLIC
Employees
201-500
Open Jobs
0

Pipeline & Clinical Trials

Clinical Trials (1)
NCT04623281Haemodialysis Outcomes & Patient Empowerment Study 02
N/A
Hemosphere platform® together with the FloTrac Acumen IQ® sensor
Intraoperative Hypotension
N/A
Clinical Trials (1)
NCT04301102The Predict H Trial
N/A
PrenaBelt
Sleep
N/A
Clinical Trials (1)
NCT02377817Halifax PrenaBelt Trial
N/A
Clinical Trials (1)
NCT04067622Novel Arm Restraint For Critically Ill Patients To Reduce Immobility, Sedation, Agitation and Cognitive Impairment
N/A
Emotion induction using video
Emotion, Expressed
N/A
Clinical Trials (1)
NCT04044261Study of Evoked Emotional Responses
N/A
Microbiological studies
Bacteremia by Enterobacteriaceae
N/A
Clinical Trials (1)
NCT02005159Study of the Impact of the Minimum Inhibitory Concentration and Susceptible Cut-off Points (CLSI, EUCAST, and Pharmacokinetics/Pharmacodynamics)in Prognosis of Bacteremia by Enterobacteriaceae
N/A
Intervention: Mental Health Technician
Depression
N/A
Clinical Trials (1)
NCT02345122CAMH PARTNERs Integrated Care Study
N/A
Register of Telaprevir and Boceprevir in Routine Clinical Practice
Hepatitis C
N/A
Clinical Trials (1)
NCT02004379Register of Telaprevir and Boceprevir in Routine Clinical Practice
N/A
Molecular Reclassification to Find Clinically Useful Biomarkers for Systemic Autoimmune Diseases: Ca
Healthy Subjects
N/A
SOONER Video & Kit
Opioid Use
N/A
Clinical Trials (1)
NCT04740099Surviving Opioid Overdose With Naloxone Education and Resuscitation Trial (SOONER)
N/A
Retrospective Observational Study to Define HBsAg Loss With or Without Seroconversion to antiHBs in
Chronic Hepatitis B Treated With Nucleoside/Nucleotide Analogues
N/A
Clinical Trials (1)
NCT02005146Retrospective Observational Study to Define HBsAg Loss With or Without Seroconversion to antiHBs in Patients With Chronic Hepatitis by B Virus Treated With Nucleoside/Nucleotide Analogs
N/A
Telemonitoring Constant
Chronic Lung Disease
N/A
Clinical Trials (1)
NCT03018717Integral Clinical Plan Shared With or Without Telemonitoring of Constants in Patient With Chronic Diseases
N/A
Standard intervention: Offer PrEP choice
Oral Pre-exposure Prophylaxis (PrEP)
N/A
Clinical Trials (1)
NCT06319105PathToScale: An Implementation Evaluation
N/A
Cone Beam Computed Tomography
Healthy Ankle
N/A
Clinical Trials (1)
NCT03619382An Evaluation Of Healthy Ankle Motion And Morphology
N/A
Standard health coaching
Metabolic Syndrome
N/A
Clinical Trials (1)
NCT04262401Promoting Healthy Habits in Metabolic Syndrome
N/A
Self monitoring of blood pressure using Health Gauge Device and monthly monitoring of weight gain
Hypertension, Pregnancy-Induced
N/A
Clinical Trials (1)
NCT03858595Optimizing Gestational Weight Gain, Birth Weight and Other Perinatal Outcomes Among Pregnant Women at Risk of Hypertension in Pregnancy
N/A
Antiplatelet Therapy in Acute Coronary Syndrome(ACS). Safety and Efficacy of Switching Antiplatelet
Acute Coronary Syndrome
N/A
Clinical Trials (1)
NCT02500290Antiplatelet Therapy in Acute Coronary Syndrome(ACS). Safety and Efficacy of Switching Antiplatelet
N/A
Etanercept Survival in Elderly Population
Psoriasis
N/A
Clinical Trials (1)
NCT02503059Etanercept Survival in Elderly Population
N/A
eADAPT training
Amputation
N/A
Clinical Trials (1)
NCT04238533Enhanced Auto-Diagnostic Adaptive Precision Trainer for Myoelectric Prosthetic Users
N/A
Clinical Trials (1)
NCT05723822Effects of Walkasins on Gait Speed of Individuals With Mild Cognitive Impairments
N/A
Hemodynamic Impact on Critical Care Patients With Lung Damage Secondary to COVID-19
Covid19
N/A
Clinical Trials (1)
NCT04556864Hemodynamic Impact on Critical Care Patients With Lung Damage Secondary to COVID-19
N/A
Multicenter Intervention Program to Optimize the Clinical Management of Community-acquired Pneumonia
Community Acquired Pneumonia
N/A
Clinical Trials (1)
NCT02224716Multicenter Intervention Program to Optimize the Clinical Management of Community-acquired Pneumonia in Hospitals
N/A
Observational Translational Study
Sarcoma
N/A
Clinical Trials (1)
NCT07432932Precision Medicine Approaches for Neoadjuvant Therapy in High-risk Sarcoma Patients
N/A
Miraπ
Stroke
N/A
Clinical Trials (1)
NCT06296628Rehabilitation Device for Hand Mirror Therapy
N/A
COMMIT mHealth application
Hiv
N/A
Clinical Trials (1)
NCT04462679COMMIT HIV Trial Nepal
N/A
Clinical Trials (1)
NCT03139955Bodytrak® Feasibility Study
N/A
StayOk web application
Mental Health Disorder
N/A
Clinical Trials (1)
NCT03213327StayOK - an Innovative Measuring Instrument for the Early Identification and Treatment of Psychosocial Risks
N/A
Room configuration
Elderly, Frail
N/A
Clinical Trials (1)
NCT04003779Reconfiguring the Patient Room to Increase Patient Stability
N/A
TURBUHALER®
Asthma
N/A
Clinical Trials (1)
NCT02983994Errors in the Use of Turbuhaler and Spiromax Devices Patients With Asthma
N/A
Molecular Reclassification to Find Clinically Useful Biomarkers for Systemic Autoimmune Diseases: In
Systemic Autoimmune Diseases
N/A
Brain Computer Interface integrated HandyRehab platform
Stroke
N/A
Clinical Trials (1)
NCT06076928Brain Computer Interface (BCI) Integrated Wearable Hand Robotic Glove System for Upper Limb Stroke Rehabilitation
N/A
Clinical Trials (1)
NCT07221747PathToScale: The PERSIST Trial
N/A
Acoustic Analytic Apps for Smart Telehealth Screening - Creating a Big Data
URTI
N/A
Clinical Trials (1)
NCT03169699Acoustic Analytic Apps for Smart Telehealth Screening - Creating a Big Data
N/A
Non-Contact Sleep Quality Monitor System
Alzheimer Disease
N/A
Clinical Trials (1)
NCT06045988Automated, Assistive, Non-Contact Sleep Quality Monitor for Individuals With Alzheimer's Disease
N/A
Peer Visitation Program
Amputation
N/A
Clinical Trials (1)
NCT03326115Effectiveness of a Peer Visitation Program to Improve Patient Activation and Quality of Life During Amputation Rehabilitation
N/A
Verio Pattern Alert® activated
Diabetes Mellitus
N/A
Clinical Trials (1)
NCT02521506Clinical Efficacy of OneTouch® Verio™IQ Meter
N/A
Fourth Trimester Mobile Tool
Pregnancy Related
N/A
Clinical Trials (1)
NCT04475718Fourth Trimester - A Web-based Tool for Postpartum Care to Address the Needs of Underserved Women
N/A
COMMIT mHealth application
Depression
N/A
Clinical Trials (1)
NCT04510909COMMIT Depression Trial Nepal
N/A
Home for Life mobile application
Hip Replacement
N/A
Clinical Trials (1)
NCT03253419HotShOT: Home Safety Occupational Therapy
N/A
Development of a Decision Aid to Facilitate Ovarian Cancer Patient's Choices Regarding Biomarker CA1
Ovarian Cancer
N/A
Clinical Trials (1)
NCT03004391Development of a Decision Aid to Facilitate Ovarian Cancer Patient's Choices Regarding Biomarker CA125
N/A
experimental foot device
Balance
N/A
Clinical Trials (1)
NCT03663816Villency-Proof of Action: Foot Device, Balance and Sway, Kinematics of Walking
N/A
Hepatic Safety of Eviplera® in HIV/Hepatitis C (HCV)-Coinfected Patients Without HCV Treatment in th
Human Immunodeficiency Virus (HIV) Hepatitis C Virus (HCV) Coinfected Subjects
N/A
Clinical Trials (1)
NCT07099066Generation of Cell Banks and Biomarker Isolation From Patients With Amyotrophic Lateral Sclerosis (ALS) (HCD-SLA)
N/A
PrenaBelt
Sleep
N/A
Clinical Trials (1)
NCT02379728Ghana PrenaBelt Trial: A Positional Therapy Device to Reduce Still-Birth
N/A
Study Of Use Of Pemetrexed In Patients With Non-Small Lung Cancer Metastatic In Andalusian Public He
Carcinoma, Non-Small-Cell Lung
N/A
Clinical Trials (1)
NCT01877902Study Of Use Of Pemetrexed In Patients With Non-Small Lung Cancer Metastatic In Andalusian Public Health System
N/A
Endocuff Vision
Colorectal Neoplasms
N/A
Clinical Trials (1)
NCT03072472BowelScope: Accuracy of Detection Using ENdocuff Optimisation of Mucosal Abnormalities
N/A
Molecular Reclassification to Find Clinically Useful Biomarkers for Systemic Autoimmune Diseases:
Systemic Autoimmune Diseases
N/A
Knee OA Brace
Knee Osteoarthritis
N/A
Clinical Trials (1)
NCT01886144Effects of Bracing on Knee Osteoarthritis (OA)
N/A
Intervention Technology
Low Back Pain
N/A
Clinical Trials (1)
NCT03478007Low-Cost Tool for Compliance and Treatment-Tracking of Low Back Pain Patients
N/A
Rehabilitation combined to a digital maintenance program
Post-COVID-19 Syndrome
N/A
Clinical Trials (1)
NCT06124625Effects of Rehabilitation Combined With a Maintenance Program Compared to Rehabilitation Alone in Post-COVID-19
N/A

Open Jobs (0)

No open positions listed yet. Check their careers page directly.

Interview Prep Quick Facts
Portfolio: 46 clinical trials
SEC Filings: 2 available

Financials (FY2025)

Revenue
$0
R&D Spend
$44M22%
Net Income
-$50M
Cash
$23M