Focal Segmental Glomerulosclerosis

Nephrology
7
Pipeline Programs
4
Companies
6
Clinical Trials
3 recruiting
1
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
4
0
2
1
Early DiscoveryClinical DevelopmentMarket

On Market (1)

Approved therapies currently available

Travere Therapeutics
FILSPARIApproved
sparsentan
Travere Therapeutics
Endothelin Receptor Antagonist [EPC]oral2023

Competitive Landscape

4 companies ranked by most advanced pipeline stage

Travere Therapeutics
3 programs
2
1
1
sparsentanPhase 31 trial
RE-021Phase 21 trial
SparsentanPhase 21 trial
Active Trials
NCT01613118Completed109Est. Mar 2024
NCT05003986Recruiting67Est. Apr 2027
NCT03493685Active Not Recruiting371Est. Feb 2026
Boehringer Ingelheim
Boehringer IngelheimINGELHEIM, Germany
1 program
1
BI 764198Phase 31 trial
Active Trials
NCT07220083Recruiting286Est. Dec 2029
Amgen
AmgenTHOUSAND OAKS, CA
1 program
1
CCX140-BPhase 21 trial
Active Trials
NCT03703908Terminated5Est. Jun 2020
Akebia Therapeutics
Akebia TherapeuticsCAMBRIDGE, MA
1 program
1
PraliciguatPhase 21 trial
Active Trials
NCT07268638RecruitingEst. Jan 2028

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
Boehringer IngelheimBI 764198
Travere Therapeuticssparsentan
Akebia TherapeuticsPraliciguat
Travere TherapeuticsSparsentan
AmgenCCX140-B
Travere TherapeuticsRE-021

Clinical Trials (6)

Total enrollment: 838 patients across 6 trials

A Study to Find Out if BI 764198 Helps Adults and Adolescents With a Kidney Condition Called Focal Segmental Glomerulosclerosis (FSGS)

Start: Feb 2026Est. completion: Dec 2029286 patients
Phase 3Recruiting

Study of Sparsentan in Patients With Primary Focal Segmental Glomerulosclerosis (FSGS)

Start: Apr 2018Est. completion: Feb 2026371 patients
Phase 3Active Not Recruiting

A Study of Praliciguat in Participants With Focal Segmental Glomerulosclerosis (FSGS)

Start: Dec 2025Est. completion: Jan 2028
Phase 2Recruiting

Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases

Start: Aug 2021Est. completion: Apr 202767 patients
Phase 2Recruiting

A Study of CCX140-B in Subjects With Primary FSGS and Nephrotic Syndrome

Start: Oct 2018Est. completion: Jun 20205 patients
Phase 2Terminated

Randomized, Double-Blind, Safety and Efficacy Study of RE-021 (Sparsentan) in Focal Segmental Glomerulosclerosis

Start: Mar 2014Est. completion: Mar 2024109 patients
Phase 2Completed

Related Jobs in Nephrology

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 late-stage (Phase 3) programs — potential near-term approvals
3 actively recruiting trials targeting 838 patients
4 companies competing in this space