PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)

Cardiovascular
1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Rocket Pharmaceuticals
1 program
1
RP-A601Phase 11 trial
Active Trials
NCT05885412Recruiting9Est. Sep 2026

Trial Timeline

Clinical trial activity over time

2023
2024
2025
2026
Rocket PharmaceuticalsRP-A601

Clinical Trials (1)

Total enrollment: 9 patients across 1 trials

A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)

Start: Aug 2023Est. completion: Sep 20269 patients
Phase 1Recruiting

Related Jobs in Cardiovascular

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 9 patients
1 companies competing in this space