Rocket Pharmaceuticals(RCKTW)
NEW YORK, NY
Pharmaceutical1 H-1B visas (FY2023)Focus: Gene Therapies
Rocket Pharmaceuticals is a life sciences company focused on Gene Therapies.
Neurology
Funding Stage
PUBLIC
Open Jobs
0
Pipeline & Clinical Trials
Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)
Leukocyte Adhesion DeficiencyClinical Trials (1)
NCT06282432Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)
N/Ano intervention
Neonatal Acute Respiratory Distress Syndrome(ARDS)Clinical Trials (1)
NCT03311165Epidemiological Study of Neonatal Acute Respiratory Distress Syndrome (ARDS)
N/ANovel Pleural Fluid, Biopsy and Serum Biomarkers for the Investigation of Pleural Effusions
Respiratory DiseaseClinical Trials (1)
NCT03661801Novel Pleural Fluid, Biopsy and Serum Biomarkers for the Investigation of Pleural Effusions
N/AHeart Transplant
Danon DiseaseClinical Trials (1)
NCT05548855Natural History of Danon Disease
N/AGroup-based Acceptance and Commitment Therapy
Acute Stroke Patients With DepressionClinical Trials (1)
NCT05727358Effectiveness of Group Acceptance and Commitment Therapy in Treating Acute Stroke Patients With Depression
N/AVacuum-Based IPC
Pleural EffusionClinical Trials (1)
NCT03831386Gravity Versus Vacuum Based Indwelling Tunneled Pleural Drainage System
N/AThe Natural History of Danon Disease
Danon DiseaseClinical Trials (1)
NCT03766386The Natural History of Danon Disease
N/Ano interventions
Bronchopulmonary DysplasiaClinical Trials (1)
NCT06082414Systemic Management in Extremely Preterm and Extremely Low Birth Weight Infants
N/ADigital Pleural Manometry
Pleural Effusion, MalignantClinical Trials (1)
NCT02805062Manometry vs Clinical Assessment in the Detection of Trapped Lung in Patients With Suspected Pleural Malignancy
N/APleural procedures
Malignant Pleural EffusionClinical Trials (1)
NCT04793607Interventions for Malignant Pleural Effusions Impact on Fatigue
N/ADelayed transanal pull-through anastomosis
Rectal CancerClinical Trials (1)
NCT06662643A Clinical Trial Comparing Staged Turnbull-Cutait Pull-through Anastomosis With Direct Anastomosis Plus Prophylactic Ileostomy in the Treatment of Low Rectal Cancer After Internal Sphincter Resection
N/ASafety and efficacy assessments
Fanconi Anemia Complementation Group AClinical Trials (1)
NCT04437771Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
N/ANo intervention
Danon DiseaseClinical Trials (1)
NCT06214507Danon Disease Natural History Study
N/APKP2-ACM Natural History Study
CardiomyopathiesClinical Trials (1)
NCT06644742PKP2-ACM Natural History Study
N/AClostridium butyricum
Rectal CancerClinical Trials (1)
NCT07369830The Impact of Probiotic Intervention on the Gut Microbiota and Bowel Function
N/ADevice: Butterfly iQ
Covid19Clinical Trials (1)
NCT04967729COVID-19 and Lung Ultrasound Utility
N/ATransarterial infusion chemotherapy
Unresectable Colorectal CancerClinical Trials (1)
NCT07333053Clinical Efficacy of Transarterial Infusion Chemotherapy for Unresectable Colorectal Cancer
N/AEDIT Management
Pleural Effusion, MalignantClinical Trials (1)
NCT03319186EDIT Management Feasibility Trial
N/APhase 1
Clinical Trials (1)
NCT04525352A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis
Phase 1RP-A701 is a recombinant viral vector composed of an AAV serotype rh.74
Dilated Cardiomyopathy (DCM)Clinical Trials (1)
NCT07137338A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy
Phase 1RP-A501
Danon DiseaseClinical Trials (1)
NCT03882437Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B
Phase 1Bone Marrow Aspiration
Fanconi AnemiaClinical Trials (1)
NCT01331018Gene Therapy for Fanconi Anemia
Phase 1Phase 1
Clinical Trials (1)
NCT03825783A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I
Phase 1Phase 1
Clinical Trials (1)
NCT03814408A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
Phase 1RP-L301
Pyruvate Kinase DeficiencyClinical Trials (1)
NCT04105166Gene Therapy for Pyruvate Kinase Deficiency (PKD)
Phase 1Phase 1
Clinical Trials (1)
NCT05885412A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)
Phase 1Phase 1/2
Clinical Trials (1)
NCT03812263A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I
Phase 1/2RP-L301
Pyruvate Kinase DeficiencyClinical Trials (1)
NCT06422351Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase Deficiency
Phase 2Phase 2
Clinical Trials (1)
NCT04248439Gene Therapy for Fanconi Anemia, Complementation Group A
Phase 2RP-A501
Danon DiseaseClinical Trials (1)
NCT06092034A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Phase 2Phase 2
Clinical Trials (1)
NCT04069533Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A
Phase 2Tislelizumab
Locally Advanced Rectal CarcinomaClinical Trials (1)
NCT06312982A Series of Neoadjuvant Chemoradiotherapy Combined With Immunotherapy for Locally Advanced Rectal Cancer
Phase 2/3SIS-reinforced anastomosis
Rectal CancerClinical Trials (1)
NCT07209787SIS-Reinforced vs. Conventional Anastomosis for Mid-to-Low Rectal Cancer: A Multicenter RCT on Anastomotic Leak
Phase 4Phase 4
Clinical Trials (1)
NCT02937974Evaluate the Efficacy of Xuebijing Injection in Acute Exacerbations of COPD
Phase 4Open Jobs (0)
No open positions listed yet. Check their careers page directly.
Interview Prep Quick Facts
Portfolio: 34 clinical trials
H-1B (2023): 1 approval
SEC Filings: 2 available
Hiring Trend
Stable
0
Open Roles
+0
Added
-0
Filled/Removed
Based on last 2 crawl cycles
Visa Sponsorship
Sponsors Work Visas
H-1B Petitions (FY2023)
1
Approved
0
Denied
100%
Rate
Source: USCIS H-1B Employer Data Hub