Dilated Cardiomyopathy (DCM)

Cardiovascular
3
Pipeline Programs
3
Companies
3
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
2
1
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Gene Therapy
1100%
+ 2 programs with unclassified modality

Competitive Landscape

3 companies ranked by most advanced pipeline stage

Affinia Therapeutics
1 program
1
AFTX-201Phase 1/21 trial
Active Trials
NCT07426419Not Yet RecruitingEst. Dec 2032
Capricor Therapeutics
1 program
1
Allogeneic Cardiosphere-Derived CellsPhase 11 trial
Active Trials
NCT02293603Unknown42Est. Apr 2020
Rocket Pharmaceuticals
1 program
1
RP-A701 is a recombinant viral vector composed of an AAV serotype rh.74Phase 1Gene Therapy1 trial
Active Trials
NCT07137338Not Yet Recruiting8Est. Jun 2029

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
Affinia TherapeuticsAFTX-201
Rocket PharmaceuticalsRP-A701 is a recombinant viral vector composed of an AAV serotype rh.74
Capricor TherapeuticsAllogeneic Cardiosphere-Derived Cells

Clinical Trials (3)

Total enrollment: 50 patients across 3 trials

An AAV Gene Therapy Trial of AFTX-201 in Adults With BAG3-Associated Dilated Cardiomyopathy (DCM)

Start: Mar 2026Est. completion: Dec 2032
Phase 1/2Not Yet Recruiting
NCT07137338Rocket PharmaceuticalsRP-A701 is a recombinant viral vector composed of an AAV serotype rh.74

A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy

Start: Jun 2026Est. completion: Jun 20298 patients
Phase 1Not Yet Recruiting
NCT02293603Capricor TherapeuticsAllogeneic Cardiosphere-Derived Cells

Dilated cardiomYopathy iNtervention With Allogeneic MyocardIally-regenerative Cells (DYNAMIC)

Start: Nov 2014Est. completion: Apr 202042 patients
Phase 1Unknown

Related Jobs in Cardiovascular

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

3 companies competing in this space