Symptomatic Transthyretin Amyloid Cardiomyopathy

Cardiovascular
1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
1
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

BridgeBio Pharma
BridgeBio PharmaCA - Palo Alto
1 program
1
ALXN2060Phase 31 trial
Active Trials
NCT04622046Completed25Est. Aug 2025

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
BridgeBio PharmaALXN2060

Clinical Trials (1)

Total enrollment: 25 patients across 1 trials

A Phase 3 Study of ALXN2060 in Japanese Participants With Symptomatic ATTR-CM

Start: Nov 2020Est. completion: Aug 202525 patients
Phase 3Completed

Related Jobs in Cardiovascular

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 companies competing in this space