Myasthenia Gravis, MuSK

Neurology
2
Pipeline Programs
1
Companies
1
Clinical Trials
1
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
1
1
Early DiscoveryClinical DevelopmentMarket

On Market (1)

Approved therapies currently available

Catalyst Pharmaceuticals
FIRDAPSEApproved
amifampridine phosphate
Catalyst Pharmaceuticals
oral2018

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Catalyst Pharmaceuticals
Catalyst PharmaceuticalsCORAL GABLES, FL
1 program
1
1
Amifampridine PhosphatePhase 31 trial
Active Trials
NCT03579966TerminatedEst. Aug 2022

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Catalyst PharmaceuticalsAmifampridine Phosphate

Clinical Trials (1)

Long Term Safety Study of Amifampridine Phosphate in MuSK-MG (Muscle Specific Tyrosine Kinase Myasthenia Gravis)

Start: Jun 2018Est. completion: Aug 2022
Phase 3Terminated

Related Jobs in Neurology

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 companies competing in this space