Catalyst Pharmaceuticals(CPRX)
CORAL GABLES, FL
Pharmaceutical1 H-1B visas (FY2023)Focus: Small Molecules for Addiction Treatment
Catalyst Pharmaceuticals is a life sciences company focused on Small Molecules for Addiction Treatment.
Neurology
Funding Stage
PUBLIC
Open Jobs
4
Products & Portfolio (4)
AGAMREE
vamorolone
Growth
ORAL · SUSPENSION
anti-inflammatory and immunosuppressive effects. The precise mechanism by which vamorolone exerts its effect in patients with DMD is unknown.
Duchenne muscular dystrophy (DMD) in patients 2 years of ageolder
2023
0
FIRDAPSE
amifampridine phosphate
Peak
ORAL · TABLET
elucidated. Amifampridine is a broad-spectrum potassium channel blocker.
Lambert-Eaton myasthenic syndrome (LEMS) in adultsolder
2018
0
FYCOMPA
perampanel
LOE Approaching
ORAL · TABLET
AMPA Receptor Antagonists
2012
25
FYCOMPA
perampanel
LOE Approaching
ORAL · SUSPENSION
AMPA Receptor Antagonists
2016
25
Pipeline & Clinical Trials
Hexaminolevulinate hydrochloride
Bladder CancerClinical Trials (1)
NCT02660645Blue Light Cystoscopy With Cysview® Registry
N/AScreening Study to Identify Patients With Complement Factor I Deficiencies
Previous Diagnosis With a Complement-mediated Disease and/or With Clinical Manifestations Reasonably Associated With Complement Factor I DeficiencyClinical Trials (1)
NCT05072912Screening Study to Identify Patients With Complement Factor I Deficiencies
N/AREVIAN 101
Androgenetic AlopeciaClinical Trials (1)
NCT04019795Modulated Light Therapy in Participants With Pattern Hair Loss
N/AWondaleaf®
Other Menstruation DisordersClinical Trials (1)
NCT02857972Proof Of Concept Menstrual Hygiene Product-Wondaleaf®
N/AVamorolone
Duchenne Muscular DystrophyClinical Trials (1)
NCT06564974Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
N/Abilateral ultrasound-guided rectus sheath block
Pediatric Postoperative PainClinical Trials (1)
NCT01015053Postoperative Pain After Pediatric Umbilical Hernia Repair
N/AWondaleaf®
PregnancyClinical Trials (1)
NCT02593214Performance and Safety Trial of an Innovative Female Condom (Wondaleaf®)
N/ACatalyst CSR Total Shoulder System
Osteoarthritis Shoulder3,4-Diaminopyridine
Congenital Myasthenic SyndromeClinical Trials (1)
NCT03062631Treatment Use of 3,4 Diaminopyridine in Congenital Myasthenia
N/AStandard of Care plus Enhanced Patient Education
Aortic Valve DiseaseClinical Trials (1)
NCT06106451Optimization Post-TAVR to IMprove Activity Levels (OPTIMAL Study)
N/AA Pilot Functional Performances Study of Two Synthetic Male Condom
Functional PerformanceClinical Trials (1)
NCT03324594A Pilot Functional Performances Study of Two Synthetic Male Condom
N/AAmifampridine Phosphate
Congenital Myasthenic SyndromeClinical Trials (1)
NCT02189720Expanded Access Study Amifampridine Phosphate in Lambert-Eaton Myasthenic Syndrome (LEMS),Congenital Myasthenic Syndrome
N/AAdhesive pouch
Umbilical Cord InfectionClinical Trials (1)
NCT05569551Umbilical Cord Care in Term Neonates: The Role of Wondaleaf Adhesive Pouch (WLAP)
N/ANarrative Medicine Journaling Intervention
DSDClinical Trials (1)
NCT06989593Breaking Silence Through Story: A Narrative Medicine Intervention for Parents of Children With Urogenital Conditions
N/ANatural History Observation
Recurrent Bacterial Infection, Autoimmune DisorderClinical Trials (1)
NCT05095623A Natural History Study to Assess the Clinical Outcomes of Patients With Complement Factor I Deficiency-Mediated Disease
N/ASpencer
Medication AdherenceClinical Trials (1)
NCT04339296Connected Healthcare for Individuals Living at Home With Chronic Conditions
N/AMarzAA
Hemophilia AClinical Trials (1)
NCT04072237Study of Coagulation Faction VIIa Variant Marzeptacog Alfa (Activated) in Adult Subjects With Hemophilia
Phase 1CPP-115
Cocaine DependencyClinical Trials (1)
NCT01493596A Safety, Tolerability and Pharmacokinetic Study of CPP-115
Phase 1PF-05280602
Hemophilia AClinical Trials (1)
NCT01439971Phase 1 Safety, Pharmacokinetics And Pharmacodynamics Study Of Recombinant Factor VIIa Variant (813d) In Adult Subjects With Hemophilia
Phase 1Bumetanide
SeizuresClinical Trials (1)
NCT00830531Pilot Study of Bumetanide for Newborn Seizures
Phase 1Airway Bypass
Emphysema or COPDClinical Trials (1)
NCT06249529Airway Bypass - Safety and Feasibility Study
Phase 1ISU304/CB2679d/Dalcinonacog alfa 75~150 IU/kg
Hemophilia BClinical Trials (1)
NCT03186677Dose-escalation Study to Investigate the Safety, PK, and PD of ISU304/CB2679d in Hemophilia B Patients
Phase 1Coagulation Factor VIIa variant
Factor VII DeficiencyClinical Trials (1)
NCT04548791Study of Coagulation Factor VIIa Marzeptacog Alfa (Activated) in Subjects With Inherited Bleeding Disorders
Phase 1/2vigabatrin
Cocaine DependenceClinical Trials (1)
NCT00611130Vigabatrin for Treatment of Cocaine Dependence
Phase 2Amifampridine Phosphate
Muscular Atrophy, SpinalClinical Trials (1)
NCT03781479Controlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 Patients
Phase 2MHS-1031
Gastroesophageal RefluxClinical Trials (1)
NCT05556824Multi-Center Study of Panosyl-Isomaltooligosaccharides Adjunctive to PPI Therapy to Treat GERD
Phase 2Coagulation Factor IX variant
Hemophilia BClinical Trials (1)
NCT03995784Study of Next-Generation Recombinant Factor IX Variant in Adult Subjects With Hemophilia B
Phase 2Vigabatrin
Cocaine DependenceClinical Trials (1)
NCT00527683Double Blind Study of Vigabatrin for the Treatment of Cocaine Dependence
Phase 2Coagulation Factor VIIa variant
Hemophilia A With InhibitorClinical Trials (1)
NCT03407651Study of Coagulation Factor VIIa Variant Marzeptacog Alfa (Activated) in Adult Subjects With Hemophilia A and B
Phase 2Amifampridine Phosphate 10 MG Oral Tablet
Spinal Muscular Atrophy Type 3Clinical Trials (1)
NCT03819660Long Term Safety of Amifampridine Phosphate in Spinal Muscular Atrophy 3
Phase 2Dupilumab
COVID-19Clinical Trials (1)
NCT04920916Safety and Efficacy of Dupilumab for Treatment of Hospitalized COVID-19 Patients
Phase 2Decitabine
Acute Myeloid LeukemiaClinical Trials (1)
NCT05796570A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies
Phase 2CPP-109 vigabatrin
Methamphetamine DependenceClinical Trials (1)
NCT00730522Safety and Efficacy Study of Vigabatrin to Treat Methamphetamine Dependence
Phase 2Vigabatrin
Cocaine AddictionClinical Trials (1)
NCT01281202Vigabatrin for the Treatment of Cocaine Dependency
Phase 2/3Amifampridine Phosphate
Lambert Eaton Myasthenic SyndromeClinical Trials (1)
NCT01377922A Phase 3 Study of Amifampridine Phosphate in Patients With Lambert Eaton Myasthenic Syndrome (LEMS)
Phase 3amifampridine phosphate
Myasthenic Syndromes, CongenitalClinical Trials (1)
NCT02562066Amifampridine Phosphate for the Treatment of Congenital Myasthenic Syndromes
Phase 3Phase 3
Clinical Trials (1)
NCT04489537Study of Coagulation Factor VIIa Marzeptacog Alfa (Activated) in Subjects With Hemophilia A or B
Phase 3Amifampridine Phosphate
Myasthenia Gravis, GeneralizedClinical Trials (1)
NCT03304054Study to Evaluate Amifampridine Phosphate in Patients With MuSK-MG
Phase 3BT-001
Type2 DiabetesClinical Trials (1)
NCT05094401Use of an Investigational Digital Therapeutic in Patients With Type 2 Diabetes
Phase 3Amifampridine Phosphate
Lambert-Eaton Myasthenic SyndromeClinical Trials (1)
NCT02970162Phase 3 Study to Evaluate Efficacy of Amifampridine Phosphate in Lambert-Eaton Myasthenic Syndrome (LEMS)
Phase 3Amifampridine Phosphate
Myasthenia Gravis, MuSKClinical Trials (1)
NCT03579966Long Term Safety Study of Amifampridine Phosphate in MuSK-MG (Muscle Specific Tyrosine Kinase Myasthenia Gravis)
Phase 3Open Jobs (4)
Interview Prep Quick Facts
Portfolio: 4 approved products, 40 clinical trials
Top TAs: Neurology, Rare Diseases
H-1B (2023): 1 approval
SEC Filings: 2 available
Open Roles: 4 active jobs
Portfolio Health
Growth1 (25%)
Peak1 (25%)
LOE Approaching2 (50%)
4 total products
Financials (FY2025)
Revenue
$398M86%
R&D Spend
$93M(23%)371%
Net Income
$71MCash
$518MHiring Trend
Stable
4
Open Roles
+0
Added
-0
Filled/Removed
Based on last 4 crawl cycles
Visa Sponsorship
Sponsors Work Visas
H-1B Petitions (FY2023)
1
Approved
0
Denied
100%
Rate
Source: USCIS H-1B Employer Data Hub