Type 1 Gaucher Disease
Rare Diseases
2
Pipeline Programs
2
Companies
2
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
1
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
2 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
PfizerElelyso 60 units/kg
Amicus TherapeuticsAT2101
Clinical Trials (2)
Pharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 Gaucher Disease
Start: Jul 2019Est. completion: Jun 20200
Phase 4Withdrawn
A Study in Type 1 Gaucher Patients to Evaluate the Pharmacokinetics, Safety and Pharmacodynamics of AT2101
Start: Apr 2009Est. completion: Jul 2009
Phase 1Terminated
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Key Insights
2 companies competing in this space