Spinocerebellar Ataxia Type 2
Neurology
1
Pipeline Programs
3
Companies
2
Clinical Trials
1 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
3 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Arrowhead PharmaceuticalsARO-ATXN2 Injection
BiogenLumbar puncture
Clinical Trials (2)
Total enrollment: 76 patients across 2 trials
Study of ARO-ATXN2 Injection in Adults With Spinocerebellar Ataxia Type 2
Start: Dec 2024Est. completion: Dec 202636 patients
Phase 1Recruiting
Integrated Functional Evaluation of the Cerebellum
Start: May 2020Est. completion: Jun 202240 patients
N/ACompleted
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Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 actively recruiting trials targeting 76 patients
3 companies competing in this space