Phenylketonuria, Maternal
Rare Diseases
0
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2022
2023
2024
2025
2026
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2030
2031
BioMarin PharmaceuticalPegvaliase
Clinical Trials (1)
Total enrollment: 50 patients across 1 trials
A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeeding
Start: Nov 2022Est. completion: Oct 203250 patients
N/ARecruiting
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On Market— Approved & available
Key Insights
1 actively recruiting trials targeting 50 patients
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