Non-transfusion-dependent Thalassemia

Hematology
1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Silence Therapeutics
Silence TherapeuticsGermany - Berlin
1 program
1
SLN124Phase 11 trial
Active Trials
NCT04718844CompletedEst. May 2023

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Silence TherapeuticsSLN124

Clinical Trials (1)

NCT04718844Silence TherapeuticsSLN124

A Study Investigate the Safety, Tolerability, Pharmacokinetic, and Pharmacodynamic Response of SLN124 in Adults With Alpha/Beta-thalassaemia and Very Low- and Low-risk Myelodysplastic Syndrome

Start: Apr 2021Est. completion: May 2023
Phase 1Completed

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Phase Legend

Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available

Key Insights

1 companies competing in this space

Related Indications

Anemia(94)Myelofibrosis(23)Polycythemia Vera(18)Primary Immune Thrombocytopenia(15)Thrombocytopenia(15)Primary Myelofibrosis(14)Immune Thrombocytopenia(13)Beta-Thalassemia(11)Aplastic Anemia(7)Iron Deficiency Anemia(7)