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Immune Thrombocytopenia

Hematology
11
Pipeline Programs
19
Companies
24
Clinical Trials
7 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
2
0
7
0
1
1
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%
+ 25 programs with unclassified modality

Hematology is a $3.6B market dominated by a single blockbuster (IMBRUVICA at 65% share) with moderate consolidation among 15 companies.

$3.6B marketMature→ Stable30 products15 companies

Key Trends

  • IMBRUVICA monopoly creates revenue concentration risk but sustained peak-cycle performance
  • Multiple patent cliffs 2027-2030 will drive significant biosimilar/generic competition
  • 1,109 active trials signal robust pipeline activity in underexplored indications like myelofibrosis and platelet disorders

Career Verdict

Hematology offers solid commercial and medical affairs opportunities in a stable, high-margin market, but pipeline diversity remains limited outside oncology-adjacent BTK inhibitors.

AI-generated market analysis based on FDA, CMS, ClinicalTrials.gov, and hiring data

Market Leaders

#1IMBRUVICAStable
$2.4B
AbbVie·Peak9.0yr
#2PROMACTADeclining
$558M
Novartis·LOE Approaching1.7yr
#3AURYXIAStable
$183M
Ipsen·Peak4.2yr
#4OXBRYTAGrowing
$101M
Pfizer·Peak11.4yr
#5DOPTELETDeclining
$96M
Unknown·LOE Approaching1.2yr

Drug Class Breakdown

Protein Kinase Inhibitors
$2.4B(65%)

dominates market, stable

TPO-receptor agonists
$654M(18%)

multiple players, patent risk

Iron metabolism modulators
$183M(5%)

niche, CKD-focused

Hemoglobin polymerization inhibitors
$101M(3%)

sickle cell focused, growing

JAK2 inhibitors
$50M(1%)

myeloproliferative neoplasms, early growth

Erythropoiesis-stimulating agents
$60M(2%)

legacy class, biosimilar pressure

Leukocyte growth factors
$68M(2%)

biosimilar-saturated, mature

Career Outlook

Stable

Hematology is a stable, mature therapeutic area with predictable commercial demand but limited innovation upside. The market is defensible by IMBRUVICA (peak through 2035) and near-term patent cliff risks (2027-2030) will create managed-care and payer expertise needs. Long-term career growth depends on successful pipeline diversification beyond BTK inhibitors and late-stage pipeline expansion.

Breaking In

Enter via Clinical Operations or Medical Affairs to build hematology disease knowledge; specialize early in rare indications (ITP, myelofibrosis) where differentiation exists.

For Experienced Professionals

Experienced professionals should target Bristol Myers Squibb, Novartis, or GSK to lead patent-cliff transition strategies and next-generation mechanism adoption (JAK, TPO agonists).

In-Demand Skills

Managed care/payer strategyHematologic malignancy genetics (BTK, JAK2 mutations)TPO-receptor pharmacologyRare disease diagnosis and patient identificationBiosimilar/generic competitive strategyMedical writing for limited indication populations

Best For

Medical Science Liaison (rare disease focus)Brand Manager (specialty hematology)Managed Care DirectorClinical Operations ManagerPayer Strategy AnalystHealth Economics & Outcomes Research (HEOR) specialist

Hiring Landscape

$91K-$204K

Hematology hiring is concentrated in Commercial (24 roles, $201K avg) and Medical Affairs (15 roles, $204K avg) functions, reflecting a mature market focused on market penetration and specialist education. Labcorp, Bristol Myers Squibb, and Regeneron lead hiring, suggesting demand in diagnostics, R&D, and rare disease support. Notably low R&D hiring (7 roles, $147K avg) indicates limited pipeline-driven growth outside established players.

102
Open Roles
5
Companies Hiring
5
Departments

Top Hiring Companies

12Growing
10Growing
9Stable

By Department

Commercial(24%)
$201K
Clinical Operations(18%)
$91K
Medical Affairs(15%)
$204K
Manufacturing(7%)
$175K
R&D(7%)
$147K

Commercial and Medical Affairs roles offer highest compensation and most openings; entry-level clinical operations salaries lag at $91K, while R&D roles are scarce and lower-paid.

Competitive Landscape

19 companies ranked by most advanced pipeline stage

UNION therapeutics
UNION therapeuticsDenmark - Hellerup
4 programs
1
2
1
PrednisonePhase 41 trial
DexamethasonePhase 21 trial
Hetrombopag OlaminePhase 21 trial
PRG-1801Phase 1
Active Trials
NCT02153060Completed58Est. Aug 2015
NCT06478537Recruiting56Est. Jun 2027
NCT05522465Recruiting608Est. Aug 2026
Syneos Health
Syneos HealthNC - Morrisville
1 program
1
BT595Phase 3
Sandoz
SandozAustria - Kundl
3 programs
1
EltrombopagPhase 21 trial
Discontinuation of eltrombopagN/A1 trial
ITP Registry and Accompanying Biospecimen CollectionN/A1 trial
Active Trials
NCT01386723Terminated35
NCT05152238Recruiting1,100Est. Apr 2027
NCT01880047Completed35Est. Oct 2017
ViiV Healthcare
ViiV HealthcareNC - Durham
1 program
1
EltrombopagPhase 2
Incyte
IncyteDE - Wilmington
1 program
1
INCA000585Phase 21 trial
Active Trials
NCT07104565Recruiting56Est. Mar 2028
Shionogi
ShionogiJapan - Osaka
1 program
1
LusutrombopagPhase 21 trial
Active Trials
NCT01129024Terminated19Est. Jun 2011
Oscotec
OscotecKorea - Seongnam
1 program
1
SKI-O-703Phase 21 trial
Active Trials
NCT04056195Completed61Est. Jan 2023
Pregene Biopharma
Pregene BiopharmaChina - Shenzhen
1 program
1
PRG-1801Phase 11 trial
Active Trials
NCT06519565Recruiting6Est. Aug 2027
Swedish Orphan Biovitrum
2 programs
AvatrombopagN/A1 trial
ITP Registry and Accompanying Biospecimen CollectionN/A
Active Trials
NCT04943042Completed199Est. Jun 2025
Amgen
AmgenTHOUSAND OAKS, CA
2 programs
Differential Diagnostic of Immune ThrombocytoPenia (ITP) and Myelodysplastic Syndrome (MDS)N/A1 trial
ITP Registry and Accompanying Biospecimen CollectionN/A
Active Trials
NCT03469661Completed63Est. Apr 2021
Colorado Therapeutics
Colorado TherapeuticsCO - Louisville
1 program
Association of Platelet Parameters With Bleeding Severity in Children With ITPN/A1 trial
Active Trials
NCT03810352Completed95Est. Nov 2023
argenx
argenxBelgium - Zwijnaarde
1 program
ITP Registry and Accompanying Biospecimen CollectionN/A
Novartis
NovartisBASEL, Switzerland
1 program
ITP Registry and Accompanying Biospecimen CollectionN/A
Grifols
GrifolsNEW YORK, NY
1 program
ITP Registry and Accompanying Biospecimen CollectionN/A
Hutchmed
HutchmedChina - Hong Kong
1 program
HMPL-523PHASE_11 trial
Active Trials
NCT06291415Withdrawn0Est. Nov 2026
GSK
GSKLONDON, United Kingdom
1 program
EltrombopagPHASE_21 trial
Active Trials
NCT00902018Completed20Est. Sep 2015
Sanofi
SanofiPARIS, France
1 program
RilzabrutinibPHASE_2Small Molecule5 trials
Active Trials
NCT07007962Recruiting60Est. Dec 2028
NCT07216079Active Not Recruiting4Est. Nov 2026
NCT06984627Recruiting30Est. Sep 2026
+2 more trials
Biotest Pharmaceuticals
Biotest PharmaceuticalsGermany - Dreieich
1 program
BT595PHASE_31 trial
Active Trials
NCT02859909Completed34Est. Dec 2018
GC Biopharma
GC BiopharmaKorea - Yongin
1 program
Human immunoglobulin intravenousPHASE_31 trial
Active Trials
NCT02063789Completed81Est. Apr 2016

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
UNION therapeuticsPrednisone
SanofiRilzabrutinib
SanofiRilzabrutinib
Biotest PharmaceuticalsBT595
GC BiopharmaHuman immunoglobulin intravenous
IncyteINCA000585
SanofiRilzabrutinib
UNION therapeuticsHetrombopag Olamine
SanofiRilzabrutinib
OscotecSKI-O-703
SanofiRilzabrutinib
UNION therapeuticsDexamethasone
SandozEltrombopag
ShionogiLusutrombopag
GSKEltrombopag

Showing 15 of 24 trials with date data

Clinical Trials (24)

Total enrollment: 2,785 patients across 24 trials

Short-course High-dose Prednisone and Dexamethasone in Children With ITP

Start: Oct 2022Est. completion: Aug 2026608 patients
Phase 4Recruiting
NCT07007962SanofiRilzabrutinib

Study to Evaluate the Efficacy and Safety of Oral Rilzabrutinib in Adults With Immune Thrombocytopenia (ITP) Who Failed First-line Treatment

Start: Oct 2025Est. completion: Dec 202860 patients
Phase 3Recruiting
NCT07216079SanofiRilzabrutinib

Rilzabrutinib for the Adult Participants With Chronic ITP Who Have Completed Phase 3 Study in Japan

Start: Oct 2025Est. completion: Nov 20264 patients
Phase 3Active Not Recruiting

This Clinical Study is to Test Efficacy and Safety of BT595 in Chronic Primary Immune Thrombocytopenia (ITP)

Start: Nov 2016Est. completion: Dec 201834 patients
Phase 3Completed
NCT02063789GC BiopharmaHuman immunoglobulin intravenous

An Open Phase 3 Study of IV-Globulin SN Inj.10% to Treat Immune Thrombocytopenia

Start: Jun 2014Est. completion: Apr 201681 patients
Phase 3Completed

Study to Assess the Safety and Tolerability of Tafasitamab in Adult Participants With Primary Autoimmune Blood Cell Disorders

Start: Dec 2025Est. completion: Mar 202856 patients
Phase 2Recruiting
NCT06984627SanofiRilzabrutinib

A Study to Investigate the Efficacy and Safety of Rilzabrutinib in Adult Participants With Graves' Disease

Start: Sep 2025Est. completion: Sep 202630 patients
Phase 2Recruiting

TPO-RA Treatment on Immune Tolerance Induction of ITP Patients With Sustained Platelet Recovery After Treatment Termination

Start: Jun 2024Est. completion: Jun 202756 patients
Phase 2Recruiting
NCT04520451SanofiRilzabrutinib

Open Label Two-Arm Study to Evaluate Rilzabrutinib in IgG4-Related Disease Participants

Start: Aug 2020Est. completion: Oct 202427 patients
Phase 2Completed

Study of Oral SKI-O-703, SYK Inhibitor, in Patients With Persistent and Chronic Immune Thrombocytopenia (ITP)

Start: Oct 2019Est. completion: Jan 202361 patients
Phase 2Completed
NCT03395210SanofiRilzabrutinib

A Study of Rilzabrutinib in Adult Patients With Immune Thrombocytopenia (ITP)

Start: Mar 2018Est. completion: Dec 202586 patients
Phase 2Completed

An Investigation of Dexamethasone With Different Doses in the Management of Immune Thrombocytopenia (ITP)

Start: May 2014Est. completion: Aug 201558 patients
Phase 2Completed

Safety and Efficacy of Eltrombopag at Escalated Doses

Start: Feb 2013Est. completion: Oct 201735 patients
Phase 2Completed
NCT01129024ShionogiLusutrombopag

An Open-label Safety Study of Lusutrombopag (S-888711) in Adults With Chronic Immune Thrombocytopenia (ITP)

Start: Apr 2010Est. completion: Jun 201119 patients
Phase 2Terminated
NCT00902018GSKEltrombopag

Eltrombopag and the Bcl-extra-large (xL) Pathway in Idiopathic Thrombocytopenic Purpura (ITP)

Start: Jan 2009Est. completion: Sep 201520 patients
Phase 2Completed

Safety and Efficacy of PRG-1801 in Recurrent/Refractory Primary Immune Thrombocytopenia (ITP)

Start: Aug 2024Est. completion: Aug 20276 patients
Phase 1Recruiting

The Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of HMPL-523 in Adult Subjects With Immune Thrombocytopenia (ITP)

Start: Apr 2024Est. completion: Nov 20260
Phase 1Withdrawn
NCT06444191SanofiRilzabrutinib

Pharmacokinetics (PK) of Rilzabrutinib (PRN1008) in Healthy Japanese and Caucasian Subjects

Start: Jan 2021Est. completion: Apr 202123 patients
Phase 1Completed
NCT06444204SanofiRilzabrutinib

A Study to Evaluate the Effect of Mild and Moderate Hepatic Impairment on the Single-Dose Pharmacokinetics of Rilzabrutinib (PRN1008)

Start: Nov 2020Est. completion: Mar 202129 patients
Phase 1Completed

An Observational, Multicenter Study to Evaluate the Use and Effectiveness of Doptelet® in Patients With ITP

Start: Feb 2022Est. completion: Jun 2025199 patients
N/ACompleted
NCT05152238SandozITP Registry and Accompanying Biospecimen Collection

ITP Registry and Accompanying Biospecimen Collection

Start: Nov 2021Est. completion: Apr 20271,100 patients
N/ARecruiting
NCT03810352Colorado TherapeuticsAssociation of Platelet Parameters With Bleeding Severity in Children With ITP

Association of Platelet Parameters With Bleeding Severity in Children With ITP

Start: Mar 2019Est. completion: Nov 202395 patients
N/ACompleted
NCT03469661AmgenDifferential Diagnostic of Immune ThrombocytoPenia (ITP) and Myelodysplastic Syndrome (MDS)

Differential Diagnostic of Immune ThrombocytoPenia (ITP) and Myelodysplastic Syndrome (MDS)

Start: Apr 2018Est. completion: Apr 202163 patients
N/ACompleted
NCT01386723SandozDiscontinuation of eltrombopag

End of EXTEND: Discontinuation of Medication for Patients With Immune Thrombocytopenia

Start: Jun 201135 patients
N/ATerminated

Related Jobs in Hematology

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs, potential near-term approvals
7 actively recruiting trials targeting 2,785 patients
19 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.