Cholestatic Liver Disease (Except ALGS, PFIC, PBC and PSC)

Gastroenterology
1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
1
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Mirum Pharmaceuticals
Mirum PharmaceuticalsFOSTER CITY, CA
1 program
1
MaralixibatPhase 31 trial
Active Trials
NCT06553768Recruiting90Est. Feb 2027

Trial Timeline

Clinical trial activity over time

2024
2025
2026
2027
Mirum PharmaceuticalsMaralixibat

Clinical Trials (1)

Total enrollment: 90 patients across 1 trials

Evaluation of Maralixibat in Pruritus Associated With General Cholestatic Liver Disease (EXPAND)

Start: Oct 2024Est. completion: Feb 202790 patients
Phase 3Recruiting

Related Jobs in Gastroenterology

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 actively recruiting trials targeting 90 patients
1 companies competing in this space