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Rare Diseases Jobs
259 open positions in rare diseases
OncologyImmunologyNeurologyInfectious DiseasesCardiovascularMetabolic DiseasesGene TherapyCell Therapy
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Regulatory Manager Contractor - CMC
ProKidney
2w ago
RemoteRegulatory AffairsRare Diseases
Director, Supply Chain & External Manufacturing
Tessera Therapeutics
2w ago
Somerville, Massachusetts, United States
$186K - $239K
Supply ChainRare DiseasesExecutive
Facilities GMP Engineering Technician
RoslinCT
2w ago
Edinburgh, United Kingdom
FacilitiesRare Diseases
UltraCare Liaison - Hokkaido, Tohoku
Ultragenyx Pharmaceutical
2w ago
Hokkaido, Tohoku
CommercialRare DiseasesMID
UltraCare Liaison - Kanagawa, Shizuoka
Ultragenyx Pharmaceutical
2w ago
Kanagawa, Shizuoka
CommercialRare DiseasesMID
District Sales Manager - IgG4-Rare Disease (North East)
Amgen
2w ago
Massachusetts - Boston, US
Full-time
CommercialRare DiseasesMANAGER
Assoc. Director, Global Data Science Operations
BioCryst Pharmaceuticals
2w ago
US_North Carolina_Remote
Full-time
Data Science & AIRare DiseasesExecutive
Head of Finance, APAC
Biogen
2w ago
Shanghai, China
Full-time
Rare DiseasesExecutive
Senior Director, Global Regulatory Strategy
AstraZeneca
2w ago
Boston - MA, US
$212K - $318K
Full-time
Regulatory AffairsRare DiseasesSenior
Director, Product Communications
BioCryst Pharmaceuticals
2w ago
US_North Carolina_Remote
Full-time
Research & DevelopmentRare DiseasesExecutive
Scientist – Preclinical Team
Capricor Therapeutics
2w ago
San Diego, CA
$95K - $115K
Full-time
Capricor TherapeuticsRare DiseasesMID
MSAT Associate 2
Capricor Therapeutics
2w ago
San Diego, CA
$73K - $88K
Full-time
Capricor TherapeuticsRare DiseasesEntry
Scientist
STRM.BIO
2w ago
Rare Diseases
Research Associate
STRM.BIO
2w ago
Rare DiseasesEntry
International Brand Manager
Rhythm Pharmaceuticals
2w ago
Rare Diseases
Director, Revenue Forecasting and Commercial Performance (North America)
Rhythm Pharmaceuticals
2w ago
Rare DiseasesExecutive
Director, Regulatory Affairs - CMC
Stoke Therapeutics
2w ago
Bedford, Massachusetts, United States
$233K - $260K
Regulatory AffairsRare DiseasesExecutive
Pharmacometrics Consultant
Entrada Therapeutics
2w ago
Boston, MA
Clinical DevelopmentRare Diseases
Associate Director, Pharmacometrics
Entrada Therapeutics
2w ago
Boston, MA
$180K - $236K
Clinical DevelopmentRare DiseasesEntry
Senior Director, Quality Control
Stoke Therapeutics
2w ago
Bedford, Massachusetts, United States
$235K - $260K
Quality AssuranceRare DiseasesSenior