All Jobs

Rare Diseases Jobs

259 open positions in rare diseases

Krystal Biotech

Regional Gene Therapy Liaison - East Coast

Krystal Biotech

10m ago
Rare Diseases
Krystal Biotech

Regional Gene Therapy Liaison - East Coast

Krystal Biotech

10m ago
Rare Diseases
Stoke Therapeutics

Director, Clinical Development Operations Program Lead

Stoke Therapeutics

20m ago
Bedford, Massachusetts, United States
$236K - $260K
Clinical DevelopmentRare DiseasesSenior
Genetix Biotherapeutics

Manager, Gene Therapy Operations (GTO)

Genetix Biotherapeutics

12h ago
From $130K
RemotePatient SupplyRare Diseases
Genetix Biotherapeutics

Manager, Gene Therapy Operations (GTO)

Genetix Biotherapeutics

12h ago
Somerville, Massachusetts, United States
Patient SupplyRare Diseases
Novartis

Ultra-Rare Disease Territory Account Specialist – Denver, CO

Novartis

Yesterday
Field Sales (USA)
$132K - $246K
Full-time
Rare Diseases
Bristol Myers Squibb

Manager, Expert Scientific Writer

Bristol Myers Squibb

Yesterday
Otemachi-JP
Full-time
Rare Diseases
Novartis

Ultra-Rare Area Business Leader – Northwest

Novartis

Yesterday
Field Sales (USA)
$168K - $312K
Full-time
Rare Diseases
Novartis

Ultra-Rare Disease Territory Account Specialist – Phoenix, AZ

Novartis

Yesterday
Field Sales (USA)
$132K - $246K
Full-time
Rare Diseases
Alkeus Pharmaceuticals

Vice President, Clinical Operations

Alkeus Pharmaceuticals

Yesterday
Cambridge, MA
$300K - $320K
Clinical OperationsRare DiseasesExecutive
Alkeus Pharmaceuticals

Medical Director

Alkeus Pharmaceuticals

Yesterday
Cambridge, MA
$250K - $300K
Clinical DevelopmentRare DiseasesExecutive
B

Medical Engagement Manager – Diamyd Medical

Bonesupport

Yesterday
Stockholm, Sweden
Medical AffairsRare DiseasesMANAGER
BioCryst Pharmaceuticals

Exec. Director, Global Patient Engagement

BioCryst Pharmaceuticals

2d ago
US_North Carolina_Headquarters
Full-time
Research & DevelopmentRare DiseasesExecutive
Genetix Biotherapeutics

Sr. Director, Regulatory CMC

Genetix Biotherapeutics

4d ago
Somerville, MA
From $270K
Regulatory AffairsRare DiseasesSenior
Genetix Biotherapeutics

Associate Director, Quality Systems

Genetix Biotherapeutics

4d ago
Somerville, Massachusetts
From $165K
Quality AssuranceRare DiseasesEntry
Genetix Biotherapeutics

Sr. Process Engineer (MS&T)

Genetix Biotherapeutics

4d ago
Somerville, MA
ManufacturingRare DiseasesSenior
Biogen

Associate Director, Marketing, Patient Engagement- Rare Disease

Biogen

5d ago
Cambridge, MA
$164K - $226K
Full-time
Rare DiseasesEntry
Biogen

(Sr) Medical Science Liaison, Rare Diseases / SMA (f/m/d)

Biogen

5d ago
Munich, Germany
Full-time
Rare DiseasesSenior
Novartis

Manager, Regulatory Affairs Cell & Gene Therapies

Novartis

5d ago
Schaftenau
Full-time
Regulatory AffairsRare DiseasesMANAGER
Novartis

Tehnik v proizvodnji bioloških učinkovin (m/ž/d)

Novartis

5d ago
Mengeš
Full-time
Rare DiseasesMID