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Rare Diseases Jobs
259 open positions in rare diseases
OncologyImmunologyNeurologyInfectious DiseasesCardiovascularMetabolic DiseasesGene TherapyCell Therapy
Regional Gene Therapy Liaison - East Coast
Krystal Biotech
10m ago
Rare Diseases
Regional Gene Therapy Liaison - East Coast
Krystal Biotech
10m ago
Rare Diseases
Director, Clinical Development Operations Program Lead
Stoke Therapeutics
20m ago
Bedford, Massachusetts, United States
$236K - $260K
Clinical DevelopmentRare DiseasesSenior
Manager, Gene Therapy Operations (GTO)
Genetix Biotherapeutics
12h ago
From $130K
RemotePatient SupplyRare Diseases
Manager, Gene Therapy Operations (GTO)
Genetix Biotherapeutics
12h ago
Somerville, Massachusetts, United States
Patient SupplyRare Diseases
Ultra-Rare Disease Territory Account Specialist – Denver, CO
Novartis
Yesterday
Field Sales (USA)
$132K - $246K
Full-time
Rare Diseases
Manager, Expert Scientific Writer
Bristol Myers Squibb
Yesterday
Otemachi-JP
Full-time
Rare Diseases
Ultra-Rare Area Business Leader – Northwest
Novartis
Yesterday
Field Sales (USA)
$168K - $312K
Full-time
Rare Diseases
Ultra-Rare Disease Territory Account Specialist – Phoenix, AZ
Novartis
Yesterday
Field Sales (USA)
$132K - $246K
Full-time
Rare Diseases
Vice President, Clinical Operations
Alkeus Pharmaceuticals
Yesterday
Cambridge, MA
$300K - $320K
Clinical OperationsRare DiseasesExecutive
Medical Director
Alkeus Pharmaceuticals
Yesterday
Cambridge, MA
$250K - $300K
Clinical DevelopmentRare DiseasesExecutive
B
Medical Engagement Manager – Diamyd Medical
Bonesupport
Yesterday
Stockholm, Sweden
Medical AffairsRare DiseasesMANAGER
Exec. Director, Global Patient Engagement
BioCryst Pharmaceuticals
2d ago
US_North Carolina_Headquarters
Full-time
Research & DevelopmentRare DiseasesExecutive
Sr. Director, Regulatory CMC
Genetix Biotherapeutics
4d ago
Somerville, MA
From $270K
Regulatory AffairsRare DiseasesSenior
Associate Director, Quality Systems
Genetix Biotherapeutics
4d ago
Somerville, Massachusetts
From $165K
Quality AssuranceRare DiseasesEntry
Sr. Process Engineer (MS&T)
Genetix Biotherapeutics
4d ago
Somerville, MA
ManufacturingRare DiseasesSenior
Associate Director, Marketing, Patient Engagement- Rare Disease
Biogen
5d ago
Cambridge, MA
$164K - $226K
Full-time
Rare DiseasesEntry
(Sr) Medical Science Liaison, Rare Diseases / SMA (f/m/d)
Biogen
5d ago
Munich, Germany
Full-time
Rare DiseasesSenior
Manager, Regulatory Affairs Cell & Gene Therapies
Novartis
5d ago
Schaftenau
Full-time
Regulatory AffairsRare DiseasesMANAGER
Tehnik v proizvodnji bioloških učinkovin (m/ž/d)
Novartis
5d ago
Mengeš
Full-time
Rare DiseasesMID