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Rare Diseases Jobs in Biotech & Pharma | Formulate

Rare Diseases Jobs

442 open positions in rare diseases

Oncology Immunology Neurology Infectious Diseases Cardiovascular Metabolic Diseases Gene Therapy Cell Therapy

Sr. Medical Science Liaison-DMD (Duchenne Muscular Dystrophy)-Northeast

Catalyst Pharmaceuticals

Posted 2w ago

Remote

Condition in scope: Duchenne Muscular Dystrophy

RemoteMedical AffairsRare DiseasesSenior

H-1B · 1 FY23

Senior Director, Field Medical Excellence

Insmed

Posted 2w ago

Remote

$222K - $303K

Full-time

RemoteRare DiseasesExecutive

H-1B · 6 FY23

Sr. Director, Associate General Counsel – R&D

PTC Therapeutics

Posted 2w ago

USA - New Jersey - Warren (Hybrid)

$247K - $290K

Full-time

Research & DevelopmentRare DiseasesExecutive

H-1B · 4 FY23

Associate Scientist II, MS&T

Forge Biologics

Posted 2w ago

Columbus, Ohio

$80K - $144K

MS&TRare DiseasesEntry

H-1B · 1 FY23

Scientist II - Manager, PD Upstream

Forge Biologics

Posted 2w ago

Columbus, Ohio

$100K - $180K

ManufacturingRare DiseasesMANAGER

H-1B · 1 FY23

Lab Coordinator

Forge Biologics

Posted 2w ago

Columbus, Ohio

Quality AssuranceRare DiseasesMID

H-1B · 1 FY23

Director, Biostatistics

Fulcrum Therapeutics

Posted 2w ago

Cambridge, MA

$225K - $250K

Condition in scope: Sickle Cell Disease

Data ScienceRare DiseasesExecutive

H-1B · 1 FY23

Associate Director, HCP Marketing

Stoke Therapeutics

Posted 2w ago

Bedford, Massachusetts, United States

$201K - $251K

CommercialRare DiseasesExecutive

H-1B · 1 FY23

Quality Control Associate II, Controls

Capricor Therapeutics

Posted 2w ago

San Diego - SD1

$75K - $87K

Full-time

Condition in scope: Duchenne Muscular Dystrophy

Capricor TherapeuticsRare DiseasesEntry

H-1B · 1 FY23

Quality Control Scientist, Controls

Capricor Therapeutics

Posted 2w ago

San Diego - SD1

$95K - $115K

Full-time

Condition in scope: Duchenne Muscular Dystrophy

Capricor TherapeuticsRare DiseasesMID

H-1B · 1 FY23

Senior Director, Senior Leadership Development

Insmed

Posted 2w ago

NJ Corporate Headquarters; Philadelphia N, PA; Philadelphia C, PA (Hybrid)

$214K - $292K

Full-time

Rare DiseasesExecutive

H-1B · 6 FY23

Associate Director, Pharmacometrics, Clinical Pharmacology

Travere Therapeutics

Posted 2w ago

Remote

$150K - $195K

Full-time

RemoteClinical DevelopmentRare DiseasesExecutive

H-1B · 1 FY23

Clinical Account Manager (Manchester, NH)

Travere Therapeutics

Posted 2w ago

Remote

$162K - $211K

Full-time

Related drug: FILSPARI

RemoteCommercialRare DiseasesMANAGER

H-1B · 1 FY23

Manufacturing Associate I

Capricor Therapeutics

Posted 2w ago

San Diego - SD1

$25 - $30

Full-time

Condition in scope: Duchenne Muscular Dystrophy

Capricor TherapeuticsRare DiseasesEntry

H-1B · 1 FY23

Manufacturing Technician

Capricor Therapeutics

Posted 2w ago

San Diego - SD1

$23 - $24

Full-time

Condition in scope: Duchenne Muscular Dystrophy

Capricor TherapeuticsRare DiseasesMID

H-1B · 1 FY23

Project Manager, Technical Operations Life-cycle Management

Insmed

Posted 3w ago

NJ Corporate Headquarters (Hybrid)

$124K - $161K

Full-time

Project ManagementRare DiseasesMANAGER

H-1B · 6 FY23

Director, Medical Operations

Intellia Therapeutics

Posted 3w ago

Cambridge, MA

$207K - $253K

Full-time

Rare DiseasesExecutive

H-1B · 9 FY23

Senior Clinical Trial Specialist (PKU)

Maze Therapeutics

Posted 3w ago

South San Francisco, CA

$124K - $266K

Condition in scope: Phenylketonuria

Clinical OperationsRare DiseasesSenior

Associate Director, Regulatory Affairs

Entrada Therapeutics

Posted 3w ago

Boston, MA

$171K - $204K

Regulatory AffairsRare DiseasesExecutive

Manager, Program Management

Entrada Therapeutics

Posted 3w ago

Boston, MA

$127K - $159K

Research & DevelopmentRare DiseasesMANAGER

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