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Rare Diseases Jobs
259 open positions in rare diseases
OncologyImmunologyNeurologyInfectious DiseasesCardiovascularMetabolic DiseasesGene TherapyCell Therapy
Senior/Associate principal scientist-LVV & Plasmid
AstraZeneca
1mo ago
Suzhou – Biopharmaceutical Industrial Park
Full-time
Rare DiseasesEntry
Product Manager Jr. ( Rare Diseases: Complemento)
AstraZeneca
1mo ago
Chile - Santiago
Full-time
Rare Diseases
Product Manager Jr. ( Rare Diseases: Metabólicos)
AstraZeneca
1mo ago
Chile - Santiago
Full-time
Rare Diseases
Product Manager Jr. ( Rare Diseases: Neuro)
AstraZeneca
1mo ago
Chile - Santiago
Full-time
Rare Diseases
Senior Real World Data Statistician
AstraZeneca
1mo ago
India - Bangalore
Full-time
Rare DiseasesSenior
Quality Assurance Associate II- Quality Events Team
Capricor Therapeutics
1mo ago
San Diego, CA
$75K - $87K
Full-time
Capricor TherapeuticsRare DiseasesEntry
Rare Disease Product and Strategy Territory (RPST) Manager – Wallonia & Luxembourg
AstraZeneca
1mo ago
Belgium - Uccle
Full-time
Rare Diseases
HR Operations & Payroll Analyst
BioCryst Pharmaceuticals
1mo ago
US_North Carolina_Remote
Full-time
Rare Diseases
Director, Marketing Operations & Meetings
Stoke Therapeutics
1mo ago
Bedford, Massachusetts, United States
$230K - $252K
CommercialRare DiseasesExecutive
Facilities Associate II / III
Capricor Therapeutics
1mo ago
San Diego, CA
$73K - $88K
Full-time
Capricor TherapeuticsRare DiseasesEntry
Vice President, Clinical Operations
Stoke Therapeutics
1mo ago
Bedford, Massachusetts, United States
$311K - $374K
Clinical DevelopmentRare DiseasesExecutive
Associate Medical Director, Neurology Clinical Development
Stoke Therapeutics
1mo ago
Bedford, Massachusetts, United States
$269K - $331K
Clinical DevelopmentRare DiseasesEntry
Director, Product and Corporate Communications
Stoke Therapeutics
1mo ago
Bedford, Massachusetts, United States
$209K - $243K
Corporate AffairsRare DiseasesExecutive
Clinical Research Director (CRD), Rare Diseases
Sanofi
1mo ago
Cambridge, MA
$206K - $298K
Full-time
Rare DiseasesExecutive
Clinical Quality Assurance – GCP Specialist
Capricor Therapeutics
1mo ago
San Diego, CA
$109K - $118K
Full-time
Capricor TherapeuticsRare DiseasesMID
Vice President, Medical Affairs
Alkeus Pharmaceuticals
1mo ago
Cambridge, MA
$310K - $390K
Medical AffairsRare DiseasesExecutive
Senior Manager, Regulatory Affairs Project Management
Travere Therapeutics
1mo ago
Rapperswil-Jona (SG), Switzerland
Full-time
Regulatory AffairsRare DiseasesSenior
Manager, Regional Regulatory Strategist
Moderna
1mo ago
London - England
Full-time
Rare Diseases
Bioinformatician
Healx
2mo ago
Cambridge
Full-time
Pre-ClinicalRare DiseasesMID
Case Manager, Patient Services (Rare Disease)
PTC Therapeutics
2mo ago
Remote
$75K - $96K
Full-time
RemoteCommercialRare DiseasesMANAGER