ALS (Amyotrophic Lateral Sclerosis)
Neurology
2
Pipeline Programs
3
Companies
6
Clinical Trials
2 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
1
0
0
0
Early DiscoveryClinical DevelopmentMarket
Drug Modality Breakdown
RNA Therapeutic
1100%
+ 3 programs with unclassified modality
Competitive Landscape
3 companies ranked by most advanced pipeline stage
CognixionCA - Santa Barbara
2 programsCognixion + Apple Vision ProN/A1 trial
Cognixion ONEN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
2027
2028
BiogenTofersen
BiogenTofersen
KadimastemAstroRx
BiogenTofersen
CognixionCognixion + Apple Vision Pro
CognixionCognixion ONE
Clinical Trials (6)
Total enrollment: 193 patients across 6 trials
Long-Term Evaluation of BIIB067 (Tofersen)
Start: Mar 2017Est. completion: Aug 2024139 patients
Phase 3Completed
Tofersen in Non-SOD1 ALS
Start: Dec 2025Est. completion: May 202830 patients
Phase 2Recruiting
A Study to Evaluate Transplantation of Astrocytes Derived From Human Embryonic Stem Cells, in Patients With Amyotrophic Lateral Sclerosis (ALS)
Start: Apr 2018Est. completion: Jun 202016 patients
Phase 1/2Completed
A Study to Evaluate Safety, Tolerability, and Distribution of a Microdose of Radiolabeled BIIB067 (99mTc-MAG3-BIIB067) Co-administered With BIIB067 (Tofersen) to Healthy Adults
Start: Dec 2018Est. completion: Jul 20218 patients
Phase 1Completed
Augmented Reality BCI Longitudinal Study for Persons With ALS, Stroke, TBI and SCI Utilizing Cognixion + Apple Vision Pro
Start: Oct 2025Est. completion: May 2026
N/ANot Yet Recruiting
Augmented Reality BCI Longitudinal Study for Persons With Late Stage ALS
Start: Jan 2025Est. completion: Oct 2025
N/ARecruiting
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Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
2 actively recruiting trials targeting 193 patients
3 companies competing in this space