Hematologic Malignancy

8
Pipeline Programs
9
Companies
10
Clinical Trials
2 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
5
1
1
0
1
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

8 companies ranked by most advanced pipeline stage

Novartis
NovartisBASEL, Switzerland
1 program
1
PelabresibPhase 31 trial
Active Trials
NCT06401356Recruiting50Est. Jun 2027
Jazz Pharmaceuticals
Jazz PharmaceuticalsCA - Palo Alto
2 programs
1
1
FludarabinePhase 21 trial
CPX-351Phase 11 trial
Active Trials
NCT03555955Completed21Est. May 2021
NCT02718755Withdrawn0Est. May 2022
Mereo BioPharma
Mereo BioPharmaUK - London
1 program
1
MPH966Phase 1/21 trial
Active Trials
NCT03986086WithdrawnEst. Dec 2023
CT
2 programs
2
TQB3702 tabletsPhase 11 trial
TQB3909 tabletsPhase 11 trial
Active Trials
NCT05610202UnknownEst. Aug 2024
NCT06211751Not Yet RecruitingEst. Jun 2026
BioCity Biopharma
BioCity BiopharmaChina - Wuxi
1 program
1
BC3402 InjectionPhase 11 trial
Active Trials
NCT05690425UnknownEst. Jun 2024
Tr1X
Tr1XCA - San Diego
1 program
1
TRX103Phase 11 trial
Active Trials
NCT06462365RecruitingEst. Apr 2027
Novo Nordisk
Novo NordiskBAGSVAERD DENMARK, Denmark
1 program
HM-PRON/A1 trial
Active Trials
NCT04757545Completed94Est. Feb 2023
CRISPR Therapeutics
1 program
Non InterventionalN/A1 trial
Active Trials
NCT06208878Enrolling By Invitation70Est. Aug 2038

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
NovartisPelabresib
Jazz PharmaceuticalsFludarabine
Mereo BioPharmaMPH966
Tr1XTRX103
Chia Tai TianQing Pharmaceutical GroupTQB3909 tablets
BioCity BiopharmaBC3402 Injection
Chia Tai TianQing Pharmaceutical GroupTQB3702 tablets
Jazz PharmaceuticalsCPX-351
CRISPR TherapeuticsNon Interventional
Novo NordiskHM-PRO

Clinical Trials (10)

Total enrollment: 235 patients across 10 trials

An Extension Study for Patients Previously Enrolled in Studies With Pelabresib

Start: Aug 2024Est. completion: Jun 202750 patients
Phase 3Recruiting

Phase II Study of Fludarabine, Cytarabine (ARA-C) and Erwinase IV in Patients With Relapsed or Refractory Hematologic Malignancies

Start: May 2018Est. completion: May 20220
Phase 2Withdrawn

MPH966 for Prevention of Graft-versus-host Disease After Allogeneic Hematopoietic Stem Cell Transplantation

Start: Sep 2021Est. completion: Dec 2023
Phase 1/2Withdrawn

Prevention of GvHD in Participants With Hematological Malignancies Undergoing Hematopoietic Stem Cell Transplant (HSCT)

Start: Apr 2024Est. completion: Apr 2027
Phase 1Recruiting

A Clinical Trial of TQB3909 Tablets Combined With TQB3702 Tablets in Patients With Hematologic Malignancy

Start: Jan 2024Est. completion: Jun 2026
Phase 1Not Yet Recruiting

A Phase I Study of BC3402 as a Single Agent in Patients With MDS and CMML

Start: Jul 2023Est. completion: Jun 2024
Phase 1Unknown

Tolerability and Pharmacokinetics Study of TQB3702 Tablets in Hematologic Tumor Subjects

Start: Nov 2022Est. completion: Aug 2024
Phase 1Unknown

A Trial to Evaluate the Potential Impact of Renal Impairment on the Pharmacokinetics and Safety of CPX-351

Start: Nov 2018Est. completion: May 202121 patients
Phase 1Completed

A Long-term Follow-up Study of Subjects Who Received CRISPR CAR T Cellular Therapies

Start: Nov 2023Est. completion: Aug 203870 patients
N/AEnrolling By Invitation

Symptom Identification and Management in Patients With Hematological Malignancy During Follow-up Care

Start: Feb 2021Est. completion: Feb 202394 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
2 actively recruiting trials targeting 235 patients
9 companies competing in this space