NDAORALTABLET, FOR SUSPENSIONPriority Review
Approved
Mar 2010
Lifecycle
LOE Approaching
Competitive Pressure
30/100
Clinical Trials
2
Mechanism of Action
Carbamoyl Phosphate Synthetase 1 Activators
Pharmacologic Class:
Carbamoyl Phosphate Synthetase 1 Activator
Clinical Trials (2)
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Started Jun 2022
20 enrolled
HyperammonemiaMethylmalonic AcidemiaPropionic Acidemia
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
Started Jan 2019
95 enrolled
Methylmalonic AcidemiaPropionic Acidemia