Hyperammonemia
1
Pipeline Programs
2
Companies
2
Clinical Trials
1 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
2 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2022
2023
2024
2025
2026
2027
2028
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2030
2031
Liminal BioSciencesFezagepras
RecordatiCarglumic Acid
Clinical Trials (2)
Total enrollment: 20 patients across 2 trials
A Healthy Volunteer Study to Compare Fezagepras (PBI-4050) With Sodium Phenylbutyrate
Start: May 2022Est. completion: Jun 2022
Phase 1Terminated
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Start: Jun 2022Est. completion: Jun 203220 patients
N/ARecruiting
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 actively recruiting trials targeting 20 patients
2 companies competing in this space