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Targeted Therapy

1
Pipeline Programs
2
Companies
2
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%
+ 1 programs with unclassified modality

Competitive Landscape

2 companies ranked by most advanced pipeline stage

UNION therapeutics
UNION therapeuticsDenmark - Hellerup
1 program
1
Donafenib combined with paclitaxel and platinum ± PD-1 antibodyPhase 21 trial
Active Trials
NCT05310331Unknown20Est. Jun 2024
Rigel Pharmaceuticals
Rigel PharmaceuticalsSOUTH SAN FRANCISCO, CA
1 program
OlutasidenibPHASE_2Small Molecule1 trial
Active Trials
NCT07032727Recruiting68Est. Jun 2029

Trial Timeline

Clinical trial activity over time

2022
2023
2024
2025
2026
2027
2028
2029
Rigel PharmaceuticalsOlutasidenib
UNION therapeuticsDonafenib combined with paclitaxel and platinum ± PD-1 antibody

Clinical Trials (2)

Total enrollment: 88 patients across 2 trials

Olutasidenib Combined With Co-targeted Therapy in Relapsed or Refractory IDH1-mutated Myeloid Malignancies Harboring Activated Signaling Pathway Mutations

Start: Sep 2025Est. completion: Jun 202968 patients
Phase 2Recruiting
NCT05310331UNION therapeuticsDonafenib combined with paclitaxel and platinum ± PD-1 antibody

Donafenib for Recurrent Cervical Cancer

Start: Mar 2022Est. completion: Jun 202420 patients
Phase 2Unknown

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 88 patients
Small Molecule is the dominant modality (100% of programs)
2 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.