Stargardt Disease
Pipeline by Development Stage
Drug Modality Breakdown
Competitive Landscape
9 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
Showing 15 of 16 trials with date data
Clinical Trials (16)
Total enrollment: 1,338 patients across 16 trials
Study of ALK-001 on the Progression of Stargardt Disease
Safety and Efficacy of Emixustat in Stargardt Disease
A Phase 2/3 Trial to Assess the Efficacy and Safety of OCU410ST for Stargardt Disease
Phase 2/3 Study of ALK-001 in Geographic Atrophy
Safety and Effects of a Single Intravitreal Injection of vMCO-010 Optogenetic Therapy in Subjects With Stargardt Disease
Open-Label Extension: Tolerability and Effects of ALK-001 on Stargardt Disease (TEASE)
Pharmacodynamic Study of Emixustat Hydrochloride in Subjects With Macular Atrophy Secondary to Stargardt Disease
Phase 2 Tolerability and Effects of ALK-001 on Stargardt Disease
Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt Disease
A Study of AAVB-039 in Participants With Stargardt Disease (STGD1)
A Phase 1/2, First-in-Human Dose Escalation/Expansion Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of a Subretinal Injection of SB-007 in Subjects With Stargardt Disease (STGD1)
Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)
This is a Dose-finding Study Followed by 2-year Extension Study to Evaluate Safety and Tolerability of Tinlarebant in Adolescent Subjects With Stargardt Disease
Phase 1 Safety Study of ALK-001 in Healthy Volunteers
Prescreening Study to Identify Potential Stargardt Participants for ACDN-01 Clinical Trials (STARPATH)
Non-interventional Long Term Follow-up Study of Participants Previously Enrolled in the STARLIGHT Study
Phase Legend
Key Insights
The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.