SCN2A-DEE

2
Pipeline Programs
2
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
2
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Praxis Precision Medicines
1 program
1
PRAX-222 - Initial DosePhase 1/2
Precision BioSciences
1 program
1
PRAX-222 - Initial DosePhase 1/21 trial
Active Trials
NCT05737784Recruiting60Est. Sep 2027

Trial Timeline

Clinical trial activity over time

2023
2024
2025
2026
2027
Precision BioSciencesPRAX-222 - Initial Dose

Clinical Trials (1)

Total enrollment: 60 patients across 1 trials

NCT05737784Precision BioSciencesPRAX-222 - Initial Dose

A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A Developmental and Epileptic Encephalopathy

Start: Apr 2023Est. completion: Sep 202760 patients
Phase 1/2Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 60 patients
2 companies competing in this space