Primary Ciliary Dyskinesia

3
Pipeline Programs
3
Companies
5
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
2
0
1
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

3 companies ranked by most advanced pipeline stage

VP
1 program
1
VX-371Phase 21 trial
Active Trials
NCT02871778Completed123Est. Nov 2018
ReCode Therapeutics
ReCode TherapeuticsCA - Menlo Park
4 programs
2
RCT1100Phase 11 trial
RCT1100Phase 11 trial
Sano Genetics Testing KitN/A1 trial
SpirometryN/A1 trial
Active Trials
NCT06172374Active Not Recruiting150Est. Dec 2025
NCT05685186Active Not Recruiting50Est. Jun 2025
NCT06600425Completed7Est. Aug 2025
+1 more trials
Sano Genetics
Sano GeneticsUK - Cambridge
1 program
Sano Genetics Testing KitN/A

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Vertex PharmaceuticalsVX-371
ReCode TherapeuticsRCT1100
ReCode TherapeuticsRCT1100
ReCode TherapeuticsSano Genetics Testing Kit
ReCode TherapeuticsSpirometry

Clinical Trials (5)

Total enrollment: 339 patients across 5 trials

Clearing Lungs With ENaC Inhibition in Primary Ciliary Dyskinesia

Start: Aug 2016Est. completion: Nov 2018123 patients
Phase 2Completed

A Study to Assess the Safety, Tolerability, Ciliary Rescue, and Pharmacodynamics of RCT1100 in Adults With PCD

Start: Sep 2024Est. completion: Aug 20257 patients
Phase 1Completed

Study Evaluating the Safety and Tolerability of RCT1100 in Healthy and PCD Subjects

Start: Feb 2023Est. completion: Jan 20259 patients
Phase 1Completed
NCT06172374ReCode TherapeuticsSano Genetics Testing Kit

A Study Providing Genetic Testing to Find Those Who May Have Primary Ciliary Dyskinesia for Potential Clinical Trials

Start: Aug 2023Est. completion: Dec 2025150 patients
N/AActive Not Recruiting

A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults

Start: Mar 2023Est. completion: Jun 202550 patients
N/AActive Not Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

3 companies competing in this space