Neurofibromatosis 2

4
Pipeline Programs
3
Companies
39
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
4
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%
+ 3 programs with unclassified modality

Competitive Landscape

3 companies ranked by most advanced pipeline stage

AstraZeneca
AstraZenecaCAMBRIDGE, United Kingdom
2 programs
2
AZD2014Phase 21 trial
SelumetinibPhase 2Small Molecule5 trials
Active Trials
NCT02831257Completed18Est. Oct 2020
NCT03259633Approved For Marketing
NCT06360406Recruiting200Est. Sep 2031
+3 more trials
PTC Therapeutics
1 program
1
PTC299Phase 21 trial
Active Trials
NCT00911248Terminated11Est. Mar 2012
United Therapeutics
United TherapeuticsMD - Silver Spring
1 program
1
PTC299Phase 2

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaAZD2014
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib
PTC TherapeuticsPTC299
AstraZenecaSelumetinib
AstraZenecaSelumetinib
AstraZenecaSelumetinib

Showing 15 of 38 trials with date data

Clinical Trials (39)

Total enrollment: 4,492 patients across 39 trials

Selumetinib (AZD6244: ARRY-142886) (Hyd-Sulfate) in Metastatic Uveal Melanoma (SUMIT)

Start: Apr 2014Est. completion: Oct 2016152 patients
Phase 3Completed

Assess Efficacy & Safety of Selumetinib in Combination With Docetaxel in Patients Receiving 2nd Line Treatment for v-Ki-ras2 Kirsten Rat Sarcoma Viral Oncogene Homolog (KRAS) Positive NSCLC

Start: Sep 2013Est. completion: Dec 2025510 patients
Phase 3Active Not Recruiting

Comparing Complete Remission After Treatment With Selumetinib/Placebo in Patient With Differentiated Thyroid Cancer

Start: Aug 2013Est. completion: Mar 2019233 patients
Phase 3Terminated

Selumetinib in Chinese Paediatric With Post-operative NF1-PNs, PhaseⅡ, Double-Blinded, Placebo-Controlled Study

Start: Aug 2023Est. completion: Jun 20260
Phase 2Withdrawn

Trial of Selumetinib in Patients With Neurofibromatosis Type II Related Tumors

Start: May 2017Est. completion: May 202410 patients
Phase 2Terminated

AZD2014 In NF2 Patients With Progressive or Symptomatic Meningiomas

Start: Aug 2016Est. completion: Oct 202018 patients
Phase 2Completed

Selumetinib in Patients Receiving Pemetrexed and Platinum-based Chemotherapy in Advanced or Metastatic KRAS Wildtype or Unknown Non-Squamous NSCLC

Start: May 2015Est. completion: Jun 201962 patients
Phase 2Completed

Immune-Modulated Study of Selected Small Molecules (Gefitinib, AZD9291, or Selumetinib + Docetaxel) or a 1st Immune-Mediated Therapy (IMT; Tremelimumab) With a Sequential Switch to a 2nd IMT (MEDI4736) in Patients With Locally Advanced or Metastatic Non-Small-Cell Lung Cancer

Start: Jul 2014Est. completion: Jun 201632 patients
Phase 2Completed

SAFIR02_Breast - Efficacy of Genome Analysis as a Therapeutic Decision Tool for Patients With Metastatic Breast Cancer

Start: Apr 2014Est. completion: Dec 20251,460 patients
Phase 2Active Not Recruiting

Assess Efficacy and Safety of AZD6244 in Combination With Docetaxel in Patients Receiving Second Line Non Small Cell Lung Cancer Treatment.

Start: Dec 2012Est. completion: Oct 2022212 patients
Phase 2Completed

Study of Selumetinib (AZD6244)(ARRY-142886) in Combination With Irinotecan in Previously Treated Patients With Colorec

Start: Apr 2010Est. completion: Jul 201232 patients
Phase 2Completed

PTC299 for Treatment of Neurofibromatosis Type 2

Start: Jul 2009Est. completion: Mar 201211 patients
Phase 2Terminated

Intermittent Dosing Of Selumetinib In Childhood NF1 Associated Tumours

Start: Sep 2019Est. completion: Feb 202414 patients
Phase 1/2Completed

International Trial of Selumetinib in Combination With Dexamethasone for the Treatment of Acute Lymphoblastic Leukaemia

Start: May 2018Est. completion: May 202312 patients
Phase 1/2Terminated

A Study of AZD2014 in Combination With Selumetinib in Patients With Advanced Cancers

Start: Jun 2015Est. completion: Mar 2020118 patients
Phase 1/2Unknown

A Study of Selumetinib in Patients With Kaposi's Sarcoma

Start: Jun 2012Est. completion: Dec 201719 patients
Phase 1/2Terminated

Selumetinib Paediatric NF1 Japan Study

Start: Aug 2020Est. completion: Mar 202312 patients
Phase 1Completed

A Study to Evaluate Bioavailability and Food Effect of Selumetinib (AZD6244) in Healthy Male Participants

Start: Sep 2018Est. completion: Oct 201824 patients
Phase 1Completed

Selumetinib and Olaparib in Solid Tumors

Start: Aug 2017Est. completion: Aug 202690 patients
Phase 1Active Not Recruiting

Open-Label, Randomised, Multi-Drug, Biomarker-Directed, Phase 1b Study in Pts w/ Muscle Invasive Bladder Cancer

Start: Dec 2016Est. completion: Jan 2026117 patients
Phase 1Active Not Recruiting

A Study to Assess the Safety, Tolerability and Anti-tumour Activity of Ascending Doses of Selumetinib in Combination With MEDI4736 and Selumetinib in Combination With MEDI4736 and Tremelimumab in Patients With Advanced Solid Tumours

Start: Dec 2015Est. completion: Sep 201958 patients
Phase 1Completed

A Study to Assess the Relative Bioavailability of Process Variants of Selumetinib in Healthy Male Volunteers

Start: Feb 2015Est. completion: Apr 201548 patients
Phase 1Completed

A Study to Assess the Absolute Bioavailability of Oral Selumetinib in Healthy Male Volunteers.

Start: Oct 2014Est. completion: Nov 201421 patients
Phase 1Completed

AZD9291 in Combination With Ascending Doses of Novel Therapeutics

Start: Aug 2014Est. completion: Dec 2026344 patients
Phase 1Active Not Recruiting

To Assess the Effect of Itraconazole and Fluconazole on the Pharmacokinetics of Selumetinib in Healthy Male Volunteers

Start: Apr 2014Est. completion: Jun 201426 patients
Phase 1Completed

To Assess the Pharmacokinetics, Safety and Tolerability of Selumetinib in Renal Impaired Subjects and Healthy Subjects

Start: Mar 2014Est. completion: Jul 201424 patients
Phase 1Completed

To Assess the Effects of Single Oral Dose of Selumetinib [AZD6244; ARRY-142886] [Hyd-Sulfate]), on QTc Interval in Healthy Male Volunteers

Start: Mar 2014Est. completion: Aug 201454 patients
Phase 1Completed

To Assess the Effect of Rifampicin on the Pharmacokinetics of Selumetinib in Healthy Male Volunteers

Start: Feb 2014Est. completion: Apr 201424 patients
Phase 1Completed

To Assess the Effect of Food on the Pharmacokinetics of Selumetinib (AZD6244; ARRY-142886) (Hyd-Sulfate) in Healthy Male Volunteers

Start: Nov 2013Est. completion: Feb 201439 patients
Phase 1Completed

Dose-escalation Study to Assess Selumetinib Safety, Tolerability and PK

Start: Oct 2013Est. completion: May 2014117 patients
Phase 1Completed

Study Evaluating Absorption, Distribution, Metabolism and Excretion (ADME) of Single Dose [14C] Selumetinib in Volunteers

Start: Oct 2013Est. completion: Nov 20136 patients
Phase 1Completed

Selumetinib (AZD6244, ARRY-142886) J-BTC Phase 1 Study

Start: Oct 2013Est. completion: Aug 20146 patients
Phase 1Terminated

Study of Selumetinib in Patients With Previously Treated or Untreated Advanced/Metastatic NSCLC

Start: Jun 2013Est. completion: Apr 201939 patients
Phase 1Completed

ABC-04 a Study of Cisplatin, Gemcitabine and Selumetinib in Patients With Advanced Biliary Tract Cancer

Start: Feb 2012Est. completion: May 201613 patients
Phase 1Completed

A Phase I Trial of Vandetanib (AZD6474) and Selumetinib (AZD6244) for Solid Tumours Including Non Small Cell Lung Cancer (VanSel-1)

Start: Jan 2012Est. completion: Jun 202061 patients
Phase 1Completed

An Intermediate Access Protocol for Selumetinib for Treatment of Neurofibromatosis Type 1

N/AApproved For Marketing

Real-World Treatment Study of Koselugo (Selumetinib)

Start: Jun 2024Est. completion: Sep 2031200 patients
N/ARecruiting

Non-interventional Study of Patients With PN NF1 Starting Selumetinib in Russia

Start: Mar 2023Est. completion: Mar 2026150 patients
N/AActive Not Recruiting

PASS of Paediatric Patients Initiating Selumetinib

Start: May 2022Est. completion: May 2028124 patients
N/AActive Not Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 4,492 patients
3 companies competing in this space