Multiple System Atrophy

4
Pipeline Programs
4
Companies
5
Clinical Trials
3 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
2
0
1
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

Small Molecule
1100%
+ 3 programs with unclassified modality

Competitive Landscape

4 companies ranked by most advanced pipeline stage

Biohaven
BiohavenNEW HAVEN, CT
1 program
1
VerdiperstatPhase 3Small Molecule1 trial
Active Trials
NCT03952806Completed421Est. Jun 2022
AstraZeneca
AstraZenecaCAMBRIDGE, United Kingdom
1 program
1
TAK-341Phase 2
Teva
TevaIsrael - Petach Tikva
1 program
1
TEV-56286Phase 23 trials
Active Trials
NCT07197866Recruiting200Est. May 2029
NCT06627231Completed8Est. Nov 2024
NCT06568237Recruiting350Est. Sep 2027
Ionis Pharmaceuticals
1 program
1
ION464Phase 11 trial
Active Trials
NCT04165486Recruiting40Est. Sep 2027

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
2027
2028
2029
BiohavenVerdiperstat
TevaTEV-56286
TevaTEV-56286
TevaTEV-56286
Ionis PharmaceuticalsION464

Clinical Trials (5)

Total enrollment: 1,019 patients across 5 trials

Study of BHV-3241 in Participants With Multiple System Atrophy

Start: Jul 2019Est. completion: Jun 2022421 patients
Phase 3Completed

An Extension Trial to Test if TEV-56286 is Effective in Relieving Multiple System Atrophy

Start: Sep 2025Est. completion: May 2029200 patients
Phase 2Recruiting

A Trial to Test if TEV-56286 is Effective for Treatment of Participants With Multiple System Atrophy

Start: Oct 2024Est. completion: Sep 2027350 patients
Phase 2Recruiting

Mass Balance Clinical Trial With TEV-56286

Start: Oct 2024Est. completion: Nov 20248 patients
Phase 1Completed

Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of ION464 Administered to Adults With Multiple System Atrophy (HORIZON)

Start: Jul 2022Est. completion: Sep 202740 patients
Phase 1Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
3 actively recruiting trials targeting 1,019 patients
4 companies competing in this space