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Long QT Syndrome

9
Pipeline Programs
12
Companies
17
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
4
0
2
0
0
3
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

12 companies ranked by most advanced pipeline stage

Purdue Pharma
Purdue PharmaCT - Stamford
3 programs
3
ProgesteronePhase 41 trial
ProgesteronePhase 41 trial
TestosteronePhase 41 trial
Active Trials
NCT04675788Completed73Est. Apr 2025
NCT03834883Completed27Est. May 2024
NCT02513940Completed14Est. Oct 2017
QT Medical
QT MedicalCA - Diamond Bar
1 program
1
QTScreen ECG RecorderPhase 21 trial
Active Trials
NCT02412709Unknown4,000Est. Mar 2017
Innovation Pharmaceuticals
1 program
1
QTScreen ECG RecorderPhase 2
Kite Pharma
Kite PharmaCA - El Segundo
4 programs
4
EleclazinePhase 1
EleclazinePhase 1
GS-6615Phase 1
GS-6615Phase 1
Gilead Sciences
Gilead SciencesFOSTER CITY, CA
3 programs
EleclazinePHASE_12 trials
GS-6615PHASE_1
GS-6615PHASE_14 trials
Active Trials
NCT02441829Completed55Est. Dec 2015
NCT02412098Completed49Est. Apr 2016
NCT02377336Withdrawn0Est. Aug 2016
+3 more trials
Colorado Therapeutics
Colorado TherapeuticsCO - Louisville
2 programs
Dofetilide and/or sotalolN/A1 trial
Prospective Identification of Long QT Syndrome in Fetal LifeN/A
Active Trials
NCT02439658Unknown1,000Est. Apr 2023
Thryv Therapeutics
Thryv TherapeuticsQC - Montreal
2 programs
LQT-1213PHASE_11 trial
LQT-1213PHASE_1_21 trial
Active Trials
NCT05759962Completed50Est. Mar 2023
NCT05906732Terminated42Est. May 2024
Pediatrix Therapeutics
Pediatrix TherapeuticsChina - Shanghai
1 program
Multicenter Evaluation of Children and Young Adults With Genotype Positive Long QT SyndromeN/A1 trial
Active Trials
NCT01705925Completed92Est. Dec 2018
Utah Medical
Utah MedicalIreland - Dublin
1 program
Prospective Identification of Long QT Syndrome in Fetal LifeN/A1 trial
Active Trials
NCT02876380Completed25Est. Jul 2019
Human BioSciences
Human BioSciencesWV - Martinsburg
1 program
Simplified Cascade ScreeningN/A
Genome & Company
Genome & CompanyKorea - Suwon
1 program
Simplified Cascade ScreeningN/A1 trial
Active Trials
NCT03783975Terminated131Est. Dec 2022
Boston Scientific
Boston ScientificCA - Valencia
1 program
subcutaneous ICDN/A1 trial
Active Trials
NCT00399412Completed86Est. Dec 2007

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Purdue PharmaProgesterone
Purdue PharmaProgesterone
Purdue PharmaTestosterone
Gilead SciencesGS-6615
QT MedicalQTScreen ECG Recorder
Gilead SciencesGS-6615
Thryv TherapeuticsLQT-1213
Thryv TherapeuticsLQT-1213
Gilead SciencesEleclazine
Gilead SciencesEleclazine
Gilead SciencesGS-6615
Gilead SciencesGS-6615
Genome & CompanySimplified Cascade Screening
Utah MedicalProspective Identification of Long QT Syndrome in Fetal Life
Colorado TherapeuticsDofetilide and/or sotalol

Showing 15 of 17 trials with date data

Clinical Trials (17)

Total enrollment: 5,900 patients across 17 trials

Novel Approaches for Minimizing Drug-Induced QT Interval Lengthening

Start: Sep 2021Est. completion: Apr 202573 patients
Phase 4Completed

Reducing the Risk of Drug-Induced QT Interval Lengthening in Women

Start: Mar 2019Est. completion: May 202427 patients
Phase 4Completed

Influence of Testosterone Administration on Drug-Induced QT Interval Prolongation and Torsades de Pointes

Start: May 2016Est. completion: Oct 201714 patients
Phase 4Completed

Effect of Eleclazine (GS-6615) on Exercise Capacity in Subjects With Symptomatic Hypertrophic Cardiomyopathy

Start: Feb 2015Est. completion: Feb 2017172 patients
Phase 2/3Terminated
NCT02412709QT MedicalQTScreen ECG Recorder

Long QT Syndrome Screening in Newborns

Start: Jun 2015Est. completion: Mar 20174,000 patients
Phase 2Unknown

GS-6615 in Adults With Chronic Stable Angina and Coronary Artery Disease

Start: May 2015Est. completion: Aug 20160
Phase 2Withdrawn

Study of LQT-1213 on QTc-induced Prolongation in Healthy Adult Subjects (Part1) and on Congenital Long QT in Patients Diagnosed With Type 2 or 3 Long QT Syndrome (Part 2).

Start: Mar 2023Est. completion: May 202442 patients
Phase 1/2Terminated

Phase 1 Study of LQT-1213 in Healthy Adults

Start: Sep 2022Est. completion: Mar 202350 patients
Phase 1Completed

Pharmacokinetics of Eleclazine in Adults With Normal and Impaired Renal Function

Start: May 2015Est. completion: Dec 201555 patients
Phase 1Completed

Pharmacokinetics of Eleclazine in Adults With Normal and Impaired Hepatic Function

Start: Mar 2015Est. completion: Apr 201649 patients
Phase 1Completed

Effect of Oral GS-6615 on Dofetilide-Induced QT Prolongation, Safety, and Tolerability in Healthy Adults

Start: Feb 2015Est. completion: May 201560 patients
Phase 1Completed

Study of the Effect of GS-6615 in Subjects With LQT-3

Start: May 2013Est. completion: Nov 201424 patients
Phase 1Completed
NCT03783975Genome & CompanySimplified Cascade Screening

KCNQ1 Cascade Screening

Start: Mar 2019Est. completion: Dec 2022131 patients
N/ATerminated
NCT02876380Utah MedicalProspective Identification of Long QT Syndrome in Fetal Life

Prospective Identification of Long QT Syndrome in Fetal Life

Start: Nov 2014Est. completion: Jul 201925 patients
N/ACompleted
NCT02439658Colorado TherapeuticsDofetilide and/or sotalol

Genetics of QT Prolongation With Antiarrhythmics

Start: Jan 2014Est. completion: Apr 20231,000 patients
N/AUnknown
NCT01705925Pediatrix TherapeuticsMulticenter Evaluation of Children and Young Adults With Genotype Positive Long QT Syndrome

Multicenter Evaluation of Children and Young Adults With Genotype Positive Long QT Syndrome

Start: Mar 2012Est. completion: Dec 201892 patients
N/ACompleted

ECG Signal Collection From Long QT Syndrome, Wide QRS Complexes, Heart Failure, and Cardiac Resynchronization Patients

Start: Nov 2006Est. completion: Dec 200786 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

12 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.