Hypophosphatasia

4
Pipeline Programs
6
Companies
3
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
3
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

5 companies ranked by most advanced pipeline stage

Ultragenyx Pharmaceutical
1 program
1
BPS804Phase 2
Mereo BioPharma
Mereo BioPharmaUK - London
1 program
1
BPS804Phase 2
Novartis
NovartisBASEL, Switzerland
1 program
1
BPS804Phase 21 trial
Active Trials
NCT01406977Completed8Est. Sep 2012
AM-Pharma
AM-PharmaNetherlands - Utrecht
1 program
1
Ilofotase Alfa, 0.8 mg/kgPhase 1/21 trial
Active Trials
NCT05890794CompletedEst. Jul 2023
C
CENTOGENEGermany - Rostock
1 program
Unraveling Genetics of HypoPhosPhatasia (HPP Genetics)N/A1 trial
Active Trials
NCT04925804Completed16Est. Dec 2021

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
NovartisBPS804
AM-PharmaIlofotase Alfa, 0.8 mg/kg
CENTOGENEUnraveling Genetics of HypoPhosPhatasia (HPP Genetics)

Clinical Trials (3)

Total enrollment: 24 patients across 3 trials

Dose Escalation Study to Evaluate the Safety and Tolerability of Multiple Infusions of BPS804 in Adults With Hypophosphatasia (HPP)

Start: Jul 2011Est. completion: Sep 20128 patients
Phase 2Completed
NCT05890794AM-PharmaIlofotase Alfa, 0.8 mg/kg

Pilot Trial of Single Dose Ilofotase Alfa in Hypophosphatasia

Start: May 2023Est. completion: Jul 2023
Phase 1/2Completed
NCT04925804CENTOGENEUnraveling Genetics of HypoPhosPhatasia (HPP Genetics)

Unraveling Genetics of HypoPhosPhatasia (HPP Genetics)

Start: Jun 2021Est. completion: Dec 202116 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

6 companies competing in this space