Skip to main content

Hereditary Amyloidosis, Transthyretin-Related

0
Pipeline Programs
3
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

3 companies ranked by most advanced pipeline stage

Alnylam Pharmaceuticals
1 program
TTR Amyloidosis Biomarker StudyN/A
Ionis Pharmaceuticals
1 program
neurofilament light chainN/A1 trial
Active Trials
NCT05311488Completed47Est. Feb 2026
AstraZeneca
AstraZenecaCAMBRIDGE, United Kingdom
1 program
neurofilament light chainN/A

Trial Timeline

Clinical trial activity over time

2022
2023
2024
2025
2026
Ionis Pharmaceuticalsneurofilament light chain

Clinical Trials (1)

Total enrollment: 47 patients across 1 trials

NCT05311488Ionis Pharmaceuticalsneurofilament light chain

Early Detection of Neuropathy in ATTRv

Start: Feb 2022Est. completion: Feb 202647 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

3 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.