Citrin Deficiency

0
Pipeline Programs
2
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Alliance Pharmaceuticals
1 program
Multi-omics Study in Citrin DeficiencyN/A1 trial
Active Trials
NCT06895746Active Not Recruiting100Est. Dec 2026
City Therapeutics
City TherapeuticsMA - Cambridge
1 program
Multi-omics Study in Citrin DeficiencyN/A

Trial Timeline

Clinical trial activity over time

2023
2024
2025
2026
Alliance PharmaceuticalsMulti-omics Study in Citrin Deficiency

Clinical Trials (1)

Total enrollment: 100 patients across 1 trials

NCT06895746Alliance PharmaceuticalsMulti-omics Study in Citrin Deficiency

Multi-omics Study in Citrin Deficiency

Start: Apr 2023Est. completion: Dec 2026100 patients
N/AActive Not Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 companies competing in this space