Aromatic Amino Acid Decarboxylase Deficiency
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1
Clinical Trials
0
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Preclinical
Phase 1
Phase 1/2
Phase 2
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2021
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2026
PTC TherapeuticsAAV2-hAADC
Clinical Trials (1)
Total enrollment: 12 patients across 1 trials
A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion
Start: Nov 2016Est. completion: May 202212 patients
Phase 2Completed
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
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