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Aniridia

0
Pipeline Programs
2
Companies
3
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

PTC Therapeutics
2 programs
AtalurenPHASE_21 trial
AtalurenPHASE_21 trial
Active Trials
NCT04117880Withdrawn0Est. Jan 2021
NCT02647359Completed39Est. Jan 2021
Angeles Therapeutics
Angeles TherapeuticsCA - Los Angeles
1 program
Morcher iris diaphragm implantationN/A1 trial
Active Trials
NCT00812708Completed72Est. Dec 2021

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
PTC TherapeuticsAtaluren
PTC TherapeuticsAtaluren
Angeles TherapeuticsMorcher iris diaphragm implantation

Clinical Trials (3)

Total enrollment: 111 patients across 3 trials

A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation Aniridia

Start: Dec 2018Est. completion: Jan 20210
Phase 2Withdrawn

Study of Ataluren in Participants With Nonsense Mutation Aniridia

Start: Jan 2016Est. completion: Jan 202139 patients
Phase 2Completed
NCT00812708Angeles TherapeuticsMorcher iris diaphragm implantation

Clinical Evaluation of Morcher Artificial Iris Diaphragms

Start: Apr 2003Est. completion: Dec 202172 patients
N/ACompleted

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

2 companies competing in this space

The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.