Aniridia
2
Pipeline Programs
1
Companies
2
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
2
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
PTC TherapeuticsAtaluren
PTC TherapeuticsAtaluren
Clinical Trials (2)
Total enrollment: 39 patients across 2 trials
A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation Aniridia
Start: Dec 2018Est. completion: Jan 20210
Phase 2Withdrawn
Study of Ataluren in Participants With Nonsense Mutation Aniridia
Start: Jan 2016Est. completion: Jan 202139 patients
Phase 2Completed
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space