Acute Intermittent Porphyria (AIP)

1
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Drug Modality Breakdown

RNA Therapeutic
1100%

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Alnylam Pharmaceuticals
1 program
1
GivosiranPhase 1RNA Therapeutic1 trial
Active Trials
NCT03505853Completed10Est. Jan 2019

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
Alnylam PharmaceuticalsGivosiran

Clinical Trials (1)

Total enrollment: 10 patients across 1 trials

A Study to Investigate the Interaction Between Givosiran and a 5-probe Drug Cocktail in Patients With Acute Intermittent Porphyria (AIP)

Start: Apr 2018Est. completion: Jan 201910 patients
Phase 1Completed

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 companies competing in this space