ORFADIN

Peak

nitisinone

NDAORALSUSPENSION
Approved
Apr 2016
Lifecycle
Peak
Competitive Pressure
0/100
Clinical Trials
7

Mechanism of Action

Hydroxyphenylpyruvate Dioxygenase Inhibitors

Pharmacologic Class:

4-Hydroxyphenyl-Pyruvate Dioxygenase Inhibitor

Clinical Trials (5)

NCT06227429N/AWithdrawn

A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

Started Sep 2025
NCT03103568Phase 1Completed

A Study to Investigate the Potential Influence of Nitisinone on the Metabolism and the Transport of Other Drugs in Healthy Volunteers

Started Mar 2017
NCT02323529Phase 3Completed

Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1

Started Dec 2014
NCT02320084N/ACompleted

Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care

Started Sep 2013
NCT01857362Phase 1Completed

Bioequivalence of Orfadin 20 mg Compared to Orfadin 10 mg Capsules.

Started May 2013

Loss of Exclusivity

LOE Date
Feb 28, 2033
85 months away
Patent Expiry
Feb 28, 2033

Patent Records (1)

Patent #ExpiryTypeUse Code
9301932
Feb 28, 2033
Product
U-1836