KUVAN

LOE Approaching

sapropterin dihydrochloride

NDAORALTABLETPriority Review
Approved
Dec 2007
Lifecycle
LOE Approaching
Competitive Pressure
25/100
Clinical Trials
20

Mechanism of Action

BH4, the cofactor for the enzyme phenylalanine hydroxylase (PAH). PAH hydroxylates Phe through an oxidative reaction to form tyrosine. In patients with PKU, PAH activity is absent or deficient. Treatment with BH4 can activate residual PAH enzyme activity, improve the normal oxidative metabolism of…

Clinical Trials (5)

NCT02677870Phase 4Completed

The Effectiveness of Kuvan in Amish PKU Patients

Started Jan 2018
7 enrolled
Phenylketonuria
NCT03864029N/ACompleted

Retrospective Observational Safety Effectiveness With Kuvan in hpA

Started Oct 2017
26 enrolled
Tetrahydrobiopterin Deficiency
NCT01965912Phase 4Completed

Kuvan®'s Effect on the Cognition of Children With Phenylketonuria

Started Oct 2013
34 enrolled
Phenylketonuria
NCT01732471Phase 3Completed

Phase 3 Open-label Study to Evaluate the Response and Safety of Kuvan® in Subjects With Phenylketonuria

Started Nov 2012
Phenylketonuria
NCT01650909N/AWithdrawn

The Effects of Sapropterin Dihydrochloride Supplementation on in Vivo Redox Status in Patients With Classical PKU

Started Jul 2012
0
Classical Phenylketonuria(PKU)

Loss of Exclusivity

LOE Date
May 16, 2026
2 months away
Patent Expiry
May 16, 2026

Patent Records (4)

Patent #ExpiryTypeUse Code
7566462
Nov 16, 2025Expired
Product
8003126
Nov 16, 2025Expired
7566462*PED
May 16, 2026
8003126*PED
May 16, 2026