ELFABRIO

Growth

pegunigalsidase alfa

BLASINGLE-USEVIALPriority Review
Approved
May 2023
Lifecycle
Growth
Competitive Pressure
30/100

Mechanism of Action

alpha-galactosidase A. ELFABRIO provides an exogenous source of alpha-galactosidase A. ELFABRIO is internalized and transported into lysosomes where it is thought to exert enzymatic activity and reduce accumulated globotriaosylceramide (Gb3).

Pharmacologic Class:

Hydrolytic Lysosomal Neutral Glycosphingolipid-specific Enzyme