X-linked Myotubular Myopathy
Pipeline by Development Stage
Drug Modality Breakdown
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
Clinical Trials (4)
Total enrollment: 79 patients across 4 trials
A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
A Long-term Follow-up Study in Male Participants With X-linked Myotubular Myopathy Treated With ASP2957
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects
Phase Legend
Key Insights
The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.