WHIM Syndrome

3
Pipeline Programs
1
Companies
2
Clinical Trials
1
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
1
0
1
1
Early DiscoveryClinical DevelopmentMarket

On Market (1)

Approved therapies currently available

U
XOLREMDIApproved
mavorixafor
Unknown Company
CXC Chemokine Receptor 4 Antagonist [EPC]oral2024

Competitive Landscape

1 companies ranked by most advanced pipeline stage

X4 Pharmaceuticals
2 programs
1
1
MavorixaforPhase 31 trial
X4P-001Phase 21 trial
Active Trials
NCT03005327CompletedEst. Jun 2022
NCT03995108Active Not RecruitingEst. Dec 2025

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
X4 PharmaceuticalsMavorixafor
X4 PharmaceuticalsX4P-001

Clinical Trials (2)

Efficacy and Safety Study of Mavorixafor in Participants With Warts, Hypogammaglobulinemia, Infections, and Myelokathexis (WHIM) Syndrome

Start: Oct 2019Est. completion: Dec 2025
Phase 3Active Not Recruiting

A Dose Determination and Safety Study of X4P-001 (Mavorixafor) in Participants With Warts, Hypogammaglobulinemia, Infections, and Myelokathexis (WHIM) Syndrome

Start: Dec 2016Est. completion: Jun 2022
Phase 2Completed

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 companies competing in this space