Von Willebrand Diseases

1
Pipeline Programs
3
Companies
4
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
1
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Octapharma
OctapharmaAustria - Vienna
3 programs
1
WilatePhase 31 trial
Use of a postpartum diary and additional blood drawsN/A1 trial
Von Willebrand Factor-Containing ProductN/A1 trial
Active Trials
NCT04146376Recruiting110Est. Dec 2026
NCT04053699Completed56Est. Jan 2021
NCT04052698Completed43Est. Apr 2022
Takeda
TakedaTOKYO, Japan
1 program
ATHN 9: Severe VWD Natural History StudyN/A1 trial
Active Trials
NCT03853486Active Not Recruiting108Est. Jul 2026

Trial Timeline

Clinical trial activity over time

2021
2022
2023
2024
2025
2026
OctapharmaWilate
OctapharmaUse of a postpartum diary and additional blood draws
OctapharmaVon Willebrand Factor-Containing Product
TakedaATHN 9: Severe VWD Natural History Study

Clinical Trials (4)

Total enrollment: 317 patients across 4 trials

Clinical Study to Investigate the Efficacy and Safety of Wilate During Prophylaxis in Previously Treated Patients With VWD

Start: Jun 2020Est. completion: Apr 202243 patients
Phase 3Completed
NCT04146376OctapharmaUse of a postpartum diary and additional blood draws

Von Willebrand Factor in Pregnancy (VIP) Study

Start: Oct 2019Est. completion: Dec 2026110 patients
N/ARecruiting
NCT04053699OctapharmaVon Willebrand Factor-Containing Product

Bleeding Incidence in VWD Patients Undergoing On-Demand Treatment

Start: Jun 2019Est. completion: Jan 202156 patients
N/ACompleted
NCT03853486TakedaATHN 9: Severe VWD Natural History Study

ATHN 9: Severe VWD Natural History Study

Start: Jun 2019Est. completion: Jul 2026108 patients
N/AActive Not Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 actively recruiting trials targeting 317 patients
3 companies competing in this space