Usher Syndromes
1
Pipeline Programs
1
Companies
2
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
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2028
2029
Nacuity PharmaceuticalsNPI-001
Nacuity PharmaceuticalsNPI-001
Clinical Trials (2)
Total enrollment: 129 patients across 2 trials
A 24-Month Trial of NPI-001 for the Preservation of Photoreceptors in Retinitis Pigmentosa Associated With Usher Syndrome
Start: Aug 2026Est. completion: Feb 202980 patients
Phase 3Not Yet Recruiting
Safety and Efficacy of NPI-001 Tablets for RP Associated With Usher Syndrome
Start: Sep 2020Est. completion: Apr 202649 patients
Phase 1/2Completed
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space
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