SHANK3 Haploinsufficiency

1
Pipeline Programs
1
Companies
1
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
1
0
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

1 companies ranked by most advanced pipeline stage

Jaguar Gene Therapy
Jaguar Gene TherapyIL - Lake Forest
1 program
1
JAG201Phase 1/21 trial
Active Trials
NCT06662188Recruiting6Est. Jun 2031

Trial Timeline

Clinical trial activity over time

2024
2025
2026
2027
2028
2029
2030
2031
Jaguar Gene TherapyJAG201

Clinical Trials (1)

Total enrollment: 6 patients across 1 trials

JAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency

Start: Jan 2024Est. completion: Jun 20316 patients
Phase 1/2Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 6 patients
1 companies competing in this space