Sanfilippo Syndrome Type A

An Assessment of Chronic Synovial-Based Inflammation and Its Role With Serum Urate Levels.

Symptom Assessment in Adult Patients With Erosive GERD (Gastroesophageal Reflux Disease) or enGERD (Endoscopic-negative GERD) After Treatment With Pantoprazole (BY1023/M3-343)

Daratumumab, Bortezomib, and Dexamethasone Followed by Daratumumab, Ixazomib, and Dexamethasone in Treating Patients With Relapsed or Refractory Multiple Myeloma

Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Taste Assessment Study of SHP429 in Healthy Adult Subjects

Value of PET/MR Enterography in the Assessment of Crohn's Disease Using a Collagen-binding Radiotracer.

Assessment of Updated Educational Materials for Instanyl®

Wearable Assessments in the Clinic and Home in PD

Assessment of Immune Activation and Tolerance in Celiac Disease During Gluten Challenge

Neurobehavioral Phenotypes in MPS III

Sophisticated Assessment of Disease Burden in Patients With Fabry Disease

A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Screening Study to Identify Pediatric Patients With Hunter Syndrome Who Demonstrate Evidence of Central Nervous System (CNS) Involvement and Who Are Currently Receiving Treatment With Elaprase®