Rare Genetic Disorders
0
Pipeline Programs
1
Companies
1
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
BioMarin PharmaceuticalNOVATO, CA
1 programCollection and Storage of Human Biospecimens for Research Into Rare Diseases and Medical ConditionsN/A1 trial
Active Trials
NCT02365376Unknown
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
BioMarin PharmaceuticalCollection and Storage of Human Biospecimens for Research Into Rare Diseases and Medical Conditions
Clinical Trials (1)
NCT02365376BioMarin PharmaceuticalCollection and Storage of Human Biospecimens for Research Into Rare Diseases and Medical Conditions
Collection and Storage of Human Biospecimens for Research Into Rare Diseases and Medical Conditions
Start: Jun 2013
N/AUnknown
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space