Rare Disorders
0
Pipeline Programs
3
Companies
3
Clinical Trials
2 recruiting
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
0
0
0
0
Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
3 companies ranked by most advanced pipeline stage
UNION therapeuticsDenmark - Hellerup
2 programsAI systemN/A1 trial
AI-Assisted DiagnosisN/A1 trial
Active Trials
Alliance PharmaceuticalsUK - Wiltshire
1 programRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
UNION therapeuticsAI system
UNION therapeuticsAI-Assisted Diagnosis
Alliance PharmaceuticalsRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Clinical Trials (3)
Total enrollment: 21,299 patients across 3 trials
AI-assisted Rare Disease Diagnosis
Start: Aug 2026Est. completion: Dec 20271,056 patients
N/ARecruiting
Artificial Intelligence for General and Rare Disease Diagnosis
Start: Jun 2026Est. completion: Aug 2026243 patients
N/ACompleted
NCT01793168Alliance PharmaceuticalsRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Start: Jul 2010Est. completion: Dec 210020,000 patients
N/ARecruiting
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
2 actively recruiting trials targeting 21,299 patients
3 companies competing in this space
The information on this page is for informational purposes only and should not be used as a substitute for professional medical advice. Drug information is sourced from FDA, DailyMed, and other government databases. Adverse event data from FAERS does not establish causation. Always consult a healthcare professional for medical decisions.