Pyruvate Dehydrogenase Complex Deficiency
Pipeline by Development Stage
Competitive Landscape
4 companies ranked by most advanced pipeline stage
Trial Timeline
Clinical trial activity over time
Clinical Trials (4)
Total enrollment: 90 patients across 4 trials
Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:
Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency
Expanded Access Treatment Protocol With DCA for Patients With PDCD
Natural History Study of Pyruvate Dehydrogenase Deficiency
Phase Legend
Key Insights
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