Pseudoxanthoma Elasticum
1
Pipeline Programs
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Companies
2
Clinical Trials
0
Approved Products
Pipeline by Development Stage
Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
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1
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Early DiscoveryClinical DevelopmentMarket
Competitive Landscape
1 companies ranked by most advanced pipeline stage
DS
Daiichi SankyoChina - Shanghai
2 programs1
DS-1211bPhase 21 trial
Non InterventionalN/A1 trial
Active Trials
Trial Timeline
Clinical trial activity over time
2021
2022
2023
2024
2025
2026
Daiichi SankyoDS-1211b
Daiichi SankyoNon Interventional
Clinical Trials (2)
Total enrollment: 113 patients across 2 trials
A Study of DS-1211b in Individuals With PseudoXanthoma Elasticum
Start: Oct 2022Est. completion: Nov 202365 patients
Phase 2Completed
Pseudoxanthoma Elasticum (PXE) Natural History Biomarkers in PXE Individuals and Their Biological Non-PXE Siblings
Start: Aug 2021Est. completion: Aug 202248 patients
N/ACompleted
Phase Legend
Preclinical— Lab & animal studies
Phase 1— Safety & dosing
Phase 2— Efficacy testing
Phase 3— Large-scale trials
On Market— Approved & available
Key Insights
1 companies competing in this space