Primary Mitochondrial Disease

2
Pipeline Programs
2
Companies
2
Clinical Trials
1 recruiting
0
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
0
0
2
0
0
0
Early DiscoveryClinical DevelopmentMarket

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Abliva
AblivaSweden - Lund
1 program
1
KL1333Phase 21 trial
Active Trials
NCT05650229Recruiting180Est. Nov 2027
OMEICOS Therapeutics
OMEICOS TherapeuticsGermany - Berlin
1 program
1
OMT-28Phase 21 trial
Active Trials
NCT05972954CompletedEst. Jul 2025

Trial Timeline

Clinical trial activity over time

2022
2023
2024
2025
2026
2027
OMEICOS TherapeuticsOMT-28
AblivaKL1333

Clinical Trials (2)

Total enrollment: 180 patients across 2 trials

OMT-28 in Patients With Primary Mitochondrial Disease (PMD) (PMD-OPTION)

Start: May 2023Est. completion: Jul 2025
Phase 2Completed

Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease

Start: Dec 2022Est. completion: Nov 2027180 patients
Phase 2Recruiting

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 actively recruiting trials targeting 180 patients
2 companies competing in this space