Primary Biliary Cholangitis (PBC)

3
Pipeline Programs
2
Companies
2
Clinical Trials
1 recruiting
1
Approved Products

Pipeline by Development Stage

Preclinical
Phase 1
Phase 1/2
Phase 2
Phase 2/3
Phase 3
On Market
0
1
0
0
0
1
1
Early DiscoveryClinical DevelopmentMarket

On Market (1)

Approved therapies currently available

Ipsen
IQIRVOApproved
elafibranor
Ipsen
Peroxisome Proliferator-activated Receptor Agonist [EPC]oral2024

Competitive Landscape

2 companies ranked by most advanced pipeline stage

Ipsen
IpsenChina - Tianjin
1 program
1
1
ElafibranorPhase 31 trial
Active Trials
NCT06016842Recruiting276Est. May 2029
Parvus Therapeutics
Parvus TherapeuticsCA - South SF
1 program
1
PVT201Phase 11 trial
Active Trials
NCT06798454CompletedEst. Apr 2025

Trial Timeline

Clinical trial activity over time

2023
2024
2025
2026
2027
2028
2029
IpsenElafibranor
Parvus TherapeuticsPVT201

Clinical Trials (2)

Total enrollment: 276 patients across 2 trials

NCT06016842IpsenElafibranor

A Long-Term Study of Elafibranor in Adult Participants With Primary Biliary Cholangitis

Start: Aug 2023Est. completion: May 2029276 patients
Phase 3Recruiting

Single Ascending Dose Study to Evaluate Safety Tolerability, Pharmacokinetics, and Pharmacodynamics of PVT201 in Healthy Subjects and Patients (PBC/PSC)

Start: Oct 2024Est. completion: Apr 2025
Phase 1Completed

Phase Legend

PreclinicalLab & animal studies
Phase 1Safety & dosing
Phase 2Efficacy testing
Phase 3Large-scale trials
On MarketApproved & available

Key Insights

1 late-stage (Phase 3) programs — potential near-term approvals
1 actively recruiting trials targeting 276 patients
2 companies competing in this space